Gene therapy for Wiskott-Aldrich syndrome in a severely affected adult
对一名重度患有Wiskott-Aldrich综合征的成年人进行基因治疗
期刊:Blood
影响因子:23.1
doi:10.1182/blood-2017-04-777136
Morris, Emma C; Fox, Thomas; Chakraverty, Ronjon; Tendeiro, Rita; Snell, Katie; Rivat, Christine; Grace, Sarah; Gilmour, Kimberly; Workman, Sarita; Buckland, Karen; Butler, Katie; Chee, Ronnie; Salama, Alan D; Ibrahim, Hazem; Hara, Havinder; Duret, Cecile; Mavilio, Fulvio; Male, Frances; Bushman, Frederick D; Galy, Anne; Burns, Siobhan O; Gaspar, H Bobby; Thrasher, Adrian J