文献库，生知库 | 链接生命科学的每一步

日期影响因子

Valproic Acid Improves Antisense-Mediated Exon-Skipping Efficacy in mdx Mice.

丙戊酸可提高 mdx 小鼠中反义介导的外显子跳跃效率

期刊:International Journal of Molecular Sciences

影响因子:4.9

doi:10.3390/ijms26062583

Phongsavanh Micky, Bizot Flavien, Saoudi Amel, Gastaldi Cecile, Le Coz Olivier, Tensorer Thomas, Brisebard Elise, Garcia Luis, Goyenvalle AurÃ©lie

发表日期：2025

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Oligonucleotide Enhancing Compound Increases Tricyclo-DNA Mediated Exon-Skipping Efficacy in the Mdx Mouse Model

寡核苷酸增强化合物可提高三环DNA介导的Mdx小鼠模型外显子跳跃效率

影响因子:5.2

doi:10.3390/cells12050702

Bizot, Flavien; Fayssoil, Abdallah; Gastaldi, Cécile; Irawan, Tabitha; Phongsavanh, Xaysongkhame; Mansart, Arnaud; Tensorer, Thomas; Brisebard, Elise; Garcia, Luis; Juliano, Rudolph L; Goyenvalle, Aurélie

发表日期：2023

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Investigating the Impact of Delivery Routes for Exon Skipping Therapies in the CNS of DMD Mouse Models

研究外显子跳跃疗法递送途径对DMD小鼠模型中枢神经系统的影响

影响因子:5.2

doi:10.3390/cells12060908

Saoudi, Amel; Fergus, Claire; Gileadi, Talia; Montanaro, Federica; Morgan, Jennifer E; Kelly, Vincent P; Tensorer, Thomas; Garcia, Luis; Vaillend, Cyrille; Muntoni, Francesco; Goyenvalle, Aurélie

发表日期：2023

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Partial Restoration of Brain Dystrophin and Behavioral Deficits by Exon Skipping in the Muscular Dystrophy X-Linked (mdx) Mouse

通过外显子跳跃技术部分恢复X连锁肌营养不良症（mdx）小鼠的脑肌营养不良蛋白和行为缺陷

期刊:Annals of Neurology

影响因子:7.7

doi:10.1002/ana.26409

Zarrouki, Faouzi; Relizani, Karima; Bizot, Flavien; Tensorer, Thomas; Garcia, Luis; Vaillend, Cyrille; Goyenvalle, Aurélie

发表日期：2022

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Identifying and Avoiding tcDNA-ASO Sequence-Specific Toxicity for the Development of DMD Exon 51 Skipping Therapy

识别并避免 tcDNA-ASO 序列特异性毒性，以开发 DMD 外显子 51 跳跃疗法

期刊:Molecular Therapy-Nucleic Acids

影响因子:6.1

doi:10.1016/j.omtn.2019.11.020

Aupy, Philippine; Echevarría, Lucía; Relizani, Karima; Zarrouki, Faouzi; Haeberli, Adrian; Komisarski, Marek; Tensorer, Thomas; Jouvion, Grégory; Svinartchouk, Fedor; Garcia, Luis; Goyenvalle, Aurélie

发表日期：2020

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