日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Real-World Effectiveness and Safety of Ravulizumab in Patients With Paroxysmal Nocturnal Hemoglobinuria: Evidence From the International PNH Registry

Ravulizumab治疗阵发性睡眠性血红蛋白尿症患者的真实世界疗效和安全性:来自国际PNH注册研究的证据

Röth, Alexander; Patriquin, Christopher J; Szer, Jeff; Terriou, Louis; Patel, Ami S; Metzger, Jesse; Gustovic, Philippe; Nishimura, Jun-Ichi; Brodsky, Robert A

Efficacy and safety of danazol for pulmonary fibrosis or bone-marrow failure associated with telomere-related gene mutation

达那唑治疗与端粒相关基因突变相关的肺纤维化或骨髓衰竭的疗效和安全性

Sicre de Fontbrune, Flore; Jouneau, Stéphane; Cottin, Vincent; Prevot, Grégoire; Nunes, Hilario; Terriou, Louis; Marchand-Adam, Sylvain; Crestani, Bruno; Marcais, Ambroise; Bergeron, Anne; Debray, Marie-Pierre; Plessier, Aurélie; Lainey, Elodie; Ba, Ibrahima; Kannengiesser, Caroline; Desseaux, Kristell; Resche-Rigon, Matthieu; Biard, Lucie; Borie, Raphael

Gamma Heavy-Chain Disease Presenting with Hypercalcaemia and Ascites

以高钙血症和腹水为首发症状的γ重链病

El Boutahiri, Imane; Mrad, Kmar; Lionne, Pauline; Terriou, Louis

RAF-independent MEK mutations drive refractory histiocytic neoplasms but respond to ERK inhibition

RAF非依赖性MEK突变驱动难治性组织细胞肿瘤,但对ERK抑制剂有反应。

Eli L Diamond ,Jean-Francois Emile ,Takeshi Fujino ,Julien Haroche ,Maxim I Maron ,Alexander M Lewis ,Jahan Rahman ,Anne S Reiner ,Dana Bossert ,Marc Rosenblum ,Mariko Yabe ,Kseniya Petrova-Drus ,Jasmine H Francis ,Veronica Rotemberg ,Raajit K Rampal ,Sarah Yoo ,Anthony F Daniyan ,Sonia Mahajan ,Vaios Hatzoglou ,Robert Young ,Gary A Ulaner ,Wiebke Rösler ,Oshrat Hershkovitz-Rokah ,Ofer Shpilberg ,Roei D Mazor ,Luke Y C Chen ,Michael Singer ,M Adriana Cuibus ,Kenyon Weis ,Salima Benbarche ,Pu Zhang ,Nina Fox ,Cynthia Castro ,Steven Tittley ,Matthew Witkowski ,Fleur Cohen-Aubart ,Louis Terriou ,Maher Hanoun ,Nicolas Schleinitz ,Gabriela Sosa ,Timo Hautala ,Laure Farnault De Lassus ,Neal Rosen ,Omar Abdel-Wahab ,Benjamin H Durham

Expanding the phenotypic and genetic landscape of congenital neutropenia through whole-exome and genome sequencing

通过全外显子组和全基因组测序扩展先天性中性粒细胞减少症的表型和遗传图谱

Marti, Séverine; Pellet, Philippe; Beaupain, Blandine; Durix, Léa; Buratti, Julien; Réguerre, Yves; Aladjidi, Nathalie; Azarnoush, Saba; Clauin, Severine; Chahla, Wahid Abou; Blaison, Gilles; Bertand, Jeremy; Bodet, Damien; Brethon, Benoit; Chane-Teng, Jessica; Delafoy, Manon; Dupraz, Chrystelle; Gandemer, Virginie; Denizeau, Philippe; Goldenberg, Alice; Hirsch, Pierre; l'Haridon, Anaïs; Marie-Cardine, Aude; Vera, Gabriella; Nelken, Brigitte; Nizery, Laure; Nolla, Marie; Pasquet, Marlène; Rosain, Jérémie; Terriou, Louis; Plo, Isabelle; Donadieu, Jean; Bellanné-Chantelot, Christine

Cold Agglutinin Syndrome Secondary to Mycoplasma pneumoniae Infection in Adults: Results From a Large French Observational Study (MyCOLD Study)

成人肺炎支原体感染引起的冷凝集素综合征:一项大型法国观察性研究(MyCOLD 研究)的结果

Chevalier, Kevin; Holub, Matthieu; Palich, Romain; Blanckaert, Karine; Gilardin, Laurent; Terriou, Louis; Arnould, Bérangère; Bellaiche, Solal; Deshayes, Samuel; Mérindol, Julie; Rolland, Simon; Valentin, Simon; Amarsy, Rishma; Audia, Sylvain; Baltes, Virginie; Barret, Amaury; Cariou, Pierre-Louis; Cattelan, Jessy; Chassepot, Hortense; Chopin, Dorothée; Clément, Mélissa; Coeffier, Marine; Comont, Thibault; De Monteynard, Soline; Declerck, Charles; Durand, Pauline; Ebbo, Mikael; Galli, Gaël; Godot, Amélie; Hamrouni, Sarra; Kaeuffer, Charlotte; Kahn, Jean-Emmanuel; Lassel, Ludovic; Leautez, Sophie; Lecapitaine, Anne-Lise; Le Moal, Gwenael; Luque Paz, David; Martinot, Martin; Mrozek, Natacha; Pagis, Valentine; Perpoint, Thomas; Salle, Valéry; Viallard, Jean-François; Viguier, Clément; Mahevas, Matthieu; Godeau, Bertrand; Crickx, Etienne; Michel, Marc

Pure Red Cell Aplasia Associated With Thymic Tumors, a Nationwide Retrospective Study

胸腺肿瘤相关纯红细胞再生障碍性贫血:一项全国性回顾性研究

Hemmer, Mylène; Moinard, Sylvain; Lambotte, Olivier; Malphettes, Marion; Terriou, Louis; Lioger, Bertrand; Le Guenno, Guillaume; Viallard, Jean-François; Michel, Marc; Lobbes, Hervé

Characteristics and outcomes associated with CD2 and CD25 expression on bone marrow mast cells in patients with systemic mastocytosis

系统性肥大细胞增生症患者骨髓肥大细胞上CD2和CD25表达的特征和相关结局

Rossignol, Julien; Georgin-Lavialle, Sophie; Canioni, Danielle; Beganovic, Omer; Brouzes, Chantal; Fain, Olivier; Heiblig, Maël; Gourguechon, Clément; Guilpain, Philippe; Bulai-Livideanu, Cristina; Barete, Stéphane; Agopian, Julie; Brenet, Fabienne; Dubreuil, Patrice; Lemal, Richard; Tournilhac, Olivier; Terriou, Louis; Launay, David; Bouillet, Laurence; Chatain, Catharina; Damaj, Ghandi; Ballul, Thomas; Greco, Celine; Polivka, Laura; Frenzel, Laurent; Meni, Cécile; Bouktit, Hassiba; Benabou, Dina; Devin, Clotilde; Gaudy-Marqueste, Caroline; Gousseff, Marie; Le Mouel, Edwige; Neel, Antoine; Ranta, Dana; Jaussaud, Roland; Jo Molina, Thierry; Bruneau, Julie; Javier, Rose-Marie; Pelletier, Fabien; Castelain, Florence; Retornaz, Frederique; Cabrera, Quentin; Zunic, Patricia; Gourin, Marie Pierre; Wierzbicka-Hainaut, Ewa; Viallard, Jean François; Lavigne, Christian; Hoarau, Cyrille; Durieu, Isabelle; Dimicoli-Salazar, Sophie; Torregrosa-Diaz, Jose Miguel; Duval, Audrey; Garcelon, Nicolas; Lespinasse, Jeremie; Soria, Angèle; Chantran, Yannick; Arock, Michel; Bodemer, Christine; Lortholary, Olivier; Asnafi, Vahid; Hermine, Olivier; Lhermitte, Ludovic

Efficacy and safety of dapsone in adult primary immune thrombocytopenia

氨苯砜治疗成人原发性免疫性血小板减少症的疗效和安全性

Larue, Marion; Moulis, Guillaume; Rueter, Manuela; Audia, Sylvain; Comont, Thibault; Terriou, Louis; Viallard, Jean-François; Pan-Petesch, Brigitte; Royer, Bruno; Bonnotte, Bernard; Galicier, Lionel; Lambotte, Olivier; Lefrere, François; Cheze, Stéphane; Ebbo, Mikael; Duong, Tu-Ahn; Boutin, Emmanuelle; Languille, Laetitia; Mahevas, Matthieu; Godeau, Bertrand; Canoui-Poitrine, Florence; Michel, Marc

Diagnosis, Characteristics, and Outcome of Selective Anti-polysaccharide Antibody Deficiencies In A Retrospective Cohort of 55 Adult Patients

55例成年患者回顾性队列研究中选择性抗多糖抗体缺乏症的诊断、特征和预后

Perrard, Nicolas; Stabler, Sarah; Sanges, Sébastien; Terriou, Louis; Lamblin, Catherine; Gaillard, Sacha; Vuotto, Fanny; Chenivesse, Cécile; Mortuaire, Geoffrey; Batteux, Frédéric; Mirgot, Floriane; Collet, Aurore; Lopez, Benjamin; Dubucquoi, Sylvain; Labalette, Myriam; Hachulla, Eric; Launay, David; Lefèvre, Guillaume