Pharmacological evaluation of drug therapies in Aicardi-Goutières syndrome: insights from patient-derived neural stem cells.
Aicardi-Goutières 综合征药物治疗的药理学评价:来自患者来源的神经干细胞的启示
期刊:Frontiers in Pharmacology
影响因子:4.8
doi:10.3389/fphar.2025.1549183
Braidotti Stefania, Ferraro Rosalba Monica, Franca Raffaella, Genova Elena, Giambuzzi Francesco, Mancini Andrea, Marinozzi Valentina, Pugnetti Letizia, Zudeh Giulia, Tesser Alessandra, Tommasini Alberto, Decorti Giuliana, Giliani Silvia Clara, Stocco Gabriele