SF3B1-mutant models of RNA mis-splicing uncover UBA1 as a therapeutic target in myelodysplastic neoplasms
SF3B1突变RNA剪接错误模型揭示UBA1是骨髓增生异常综合征的治疗靶点
期刊:Leukemia
影响因子:13.4
doi:10.1038/s41375-025-02740-1
Thier, Jonas; Hofmann, Sophia; Kirchhof, Katharina M; Todisco, Gabriele; Mortera-Blanco, Teresa; Lilienthal, Ingrid; Kanellis, Dimitris C; Barbosa, Indira; Björklund, Ann-Charlotte; Deslauriers, André G; Bartek, Jiri; Herold, Nikolas; Papaemmanuil, Elli; Papapetrou, Eirini P; Hellström-Lindberg, Eva; Moura, Pedro L; Lundin, Vanessa