日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Effective hematopoietic stem cell-based gene therapy in a murine model of hereditary pulmonary alveolar proteinosis

在遗传性肺泡蛋白沉积症小鼠模型中,基于造血干细胞的基因疗法显示出良好的疗效。

Miriam Hetzel,Elena Lopez-Rodriguez,Adele Mucci,Ariane Hai Ha Nguyen,Takuji Suzuki,Kenjiro Shima,Theresa Buchegger,Sabine Dettmer,Thomas Rodt,Jens P Bankstahl,Punam Malik,Lars Knudsen,Axel Schambach,Gesine Hansen,Bruce C Trapnell,Nico Lachmann,Thomas Moritz

iPSC-Derived Macrophages Effectively Treat Pulmonary Alveolar Proteinosis in Csf2rb-Deficient Mice

iPSC 衍生的巨噬细胞可有效治疗 Csf2rb 缺乏小鼠的肺泡蛋白沉积症

Adele Mucci, Elena Lopez-Rodriguez, Miriam Hetzel, Serena Liu, Takuji Suzuki, Christine Happle, Mania Ackermann, Henning Kempf, Roman Hillje, Jessica Kunkiel, Ewa Janosz, Sebastian Brennig, Silke Glage, Jens P Bankstahl, Sabine Dettmer, Thomas Rodt, Gudrun Gohring, Bruce Trapnell, Gesine Hansen, Col