Establishing biomarkers and clinical endpoints in myotonic dystrophy type 1 (END-DM1): Protocol of an international natural history study
建立1型强直性肌营养不良症(END-DM1)的生物标志物和临床终点:一项国际自然史研究方案
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0331163
Mul, Karlien; Eichinger, Kate; Hung, Man; Sansone, Valeria A; Gagnon, Cynthia; Subramony, Sub; Roxburgh, Richard H; Hamel, Johanna; Statland, Jeffrey M; Elsheikh, Bakri; Turner, Chris; Sampson, Jacinda; Ragole, Thomas; Matthews, Emma; Schoser, Benedikt; Swenson, Andrea; Laverty, Chamindra; Shieh, Perry; Greene, Ericka P; Takahashi, Masanori; Wicklund, Matthew; Dekdebrun, Jeanne; Raymond, Jennifer; DeSpain, Erin; Thornton, Charles A; Johnson, Nicholas E