An ex vivo gene therapy approach to treat muscular dystrophy using inducible pluripotent stem cells
利用可诱导多能干细胞治疗肌营养不良症的体外基因治疗方法
期刊:Nature Communications
影响因子:14.7
doi:10.1038/ncomms2550
Antonio Filareto, Sarah Parker, Radbod Darabi, Luciene Borges, Michelina Iacovino, Tory Schaaf, Timothy Mayerhofer, Jeffrey S Chamberlain, James M Ervasti, R Scott McIvor, Michael Kyba, Rita C R Perlingeiro