Enabling endpoint development for interventional clinical trials in individuals with Angelman syndrome: a prospective, longitudinal, observational clinical study (FREESIAS)
为安格曼综合征患者介入性临床试验开发终点指标:一项前瞻性、纵向、观察性临床研究(FREESIAS)
期刊:Journal of Neurodevelopmental Disorders
影响因子:4
doi:10.1186/s11689-023-09494-w
Tjeertes, Jorrit; Bacino, Carlos A; Bichell, Terry Jo; Bird, Lynne M; Bustamante, Mariana; Crean, Rebecca; Jeste, Shafali; Komorowski, Robert W; Krishnan, Michelle L; Miller, Meghan T; Nobbs, David; Ochoa-Lubinoff, Cesar; Parkerson, Kimberly A; Rotenberg, Alexander; Sadhwani, Anjali; Shen, Mark D; Squassante, Lisa; Tan, Wen-Hann; Vincenzi, Brenda; Wheeler, Anne C; Hipp, Joerg F; Berry-Kravis, Elizabeth