Fosmetpantotenate Randomized Controlled Trial in Pantothenate Kinase-Associated Neurodegeneration
泛酸磷酸酯治疗泛酸激酶相关神经退行性疾病的随机对照试验
期刊:Movement Disorders
影响因子:7.6
doi:10.1002/mds.28392
Klopstock, Thomas; Videnovic, Aleksandar; Bischoff, Almut Turid; Bonnet, Cecilia; Cif, Laura; Comella, Cynthia; Correa-Vela, Marta; Escolar, Maria L; Fraser, Jamie L; Gonzalez, Victoria; Hermanowicz, Neal; Jech, Robert; Jinnah, Hyder A; Kmiec, Tomasz; Lang, Anthony; Martí, Maria J; Mercimek-Andrews, Saadet; Monduy, Migvis; Nimmo, Graeme A M; Perez-Dueñas, Belen; Pfeiffer, Helle Cecilie Viekilde; Planellas, Lluis; Roze, Emmanuel; Thakur, Nivedita; Tochen, Laura; Vanegas-Arroyave, Nora; Zorzi, Giovanna; Burns, Colleen; Greblikas, Feriandas