Modelling pathogenesis and treatment of familial dysautonomia using patient-specific iPSCs
利用患者特异性诱导多能干细胞构建家族性自主神经功能障碍的发病机制及治疗模型
期刊:Nature
影响因子:48.5
doi:10.1038/nature08320
Lee, Gabsang; Papapetrou, Eirini P; Kim, Hyesoo; Chambers, Stuart M; Tomishima, Mark J; Fasano, Christopher A; Ganat, Yosif M; Menon, Jayanthi; Shimizu, Fumiko; Viale, Agnes; Tabar, Viviane; Sadelain, Michel; Studer, Lorenz