日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Endothelial and neuronal engagement by AAV-BR1 gene therapy alleviates neurological symptoms and lipid deposition in a mouse model of Niemann-Pick type C2

AAV-BR1 基因治疗促进内皮细胞和神经元的结合,可缓解尼曼匹克 C2 型小鼠模型中的神经症状和脂质沉积

Charlotte Laurfelt Munch Rasmussen, Signe Frost Frederiksen, Christian Würtz Heegaard, Maj Schneider Thomsen, Eva Hede, Bartosz Laczek, Jakob Körbelin, Daniel Wüstner, Louiza Bohn Thomsen, Markus Schwaninger, Ole N Jensen, Torben Moos #, Annette Burkhart #

Upregulation of Transferrin Receptor 1 (TfR1) but Not Glucose Transporter 1 (GLUT1) or CD98hc at the Blood-Brain Barrier in Response to Valproic Acid

丙戊酸可上调血脑屏障上的转铁蛋白受体 1 (TfR1),但不上调葡萄糖转运蛋白 1 (GLUT1) 或 CD98hc

Steinunn Sara Helgudóttir, Kasper Bendix Johnsen, Lisa Greve Routhe, Charlotte Laurfelt Munch Rasmussen, Maj Schneider Thomsen, Torben Moos

Activation of glial cells induces proinflammatory properties in brain capillary endothelial cells in vitro

神经胶质细胞的激活在体外诱导脑毛细血管内皮细胞的促炎特性

Annette Burkhart #, Steinunn Sara Helgudóttir #, Yahye A Mahamed, Mikkel B Fruergaard, Julie N Holm-Jacobsen, Hulda Haraldsdóttir, Sara E Dahl, Freja Pretzmann, Lisa Greve Routhe, Kate Lambertsen, Torben Moos #, Maj Schneider Thomsen #

CDR3 Variants of the TXB2 Shuttle with Increased TfR1 Association Rate and Enhanced Brain Penetration

TXB2 穿梭机的 CDR3 变体可提高 TfR1 结合率并增强脑渗透性

Pawel Stocki, Jaroslaw Szary, Mykhaylo Demydchuk, Leandra Northall, Charlotte L M Rasmussen, Diana Bahu Logan, Aziz Gauhar, Laura Thei, Shu-Fen Coker, Torben Moos, Frank S Walsh, J Lynn Rutkowski

A novel strategy for delivering Niemann-Pick type C2 proteins across the blood-brain barrier using the brain endothelial-specific AAV-BR1 virus

利用脑内皮特异性 AAV-BR1 病毒跨血脑屏障递送尼曼匹克 C2 型蛋白的新策略

Charlotte Laurfelt Munch Rasmussen, Eva Hede, Lisa Juul Routhe, Jakob Körbelin, Steinunn Sara Helgudottir, Louiza Bohn Thomsen, Markus Schwaninger, Annette Burkhart, Torben Moos

Sortilin regulates blood-brain barrier integrity

Sortilin 调节血脑屏障的完整性

Andrea E Toth, Hans C Helms, Andras Harazin, Kasper B Johnsen, Charlotte Goldeman, Annette Burkhart, Maj S Thomsen, Paul J Kempen, Adrián Klepe, Dora V Lipka, Peter L Møller, Thomas L Andresen, Mette Nyegaard, Torben Moos, Birger Brodin, Morten S Nielsen

Mutation of Tyrosine Sites in the Human Alpha-Synuclein Gene Induces Neurotoxicity in Transgenic Mice with Soluble Alpha-Synuclein Oligomer Formation

人类 α-突触核蛋白基因酪氨酸位点突变导致转基因小鼠产生神经毒性,并形成可溶性 α-突触核蛋白寡聚体

Louise Berkhoudt Lassen, Maj Schneider Thomsen, Elisa Basso, Ernst-Martin Füchtbauer, Annette Füchtbauer, Tiago Fleming Outeiro, Poul Henning Jensen, Torben Moos

Post-capillary venules are the key locus for transcytosis-mediated brain delivery of therapeutic nanoparticles

毛细血管后小静脉是转胞吞介导治疗性纳米粒子脑输送的关键部位

Krzysztof Kucharz #, Kasper Kristensen #, Kasper Bendix Johnsen #, Mette Aagaard Lund, Micael Lønstrup, Torben Moos, Thomas Lars Andresen, Martin Johannes Lauritzen

Gene therapy to the blood-brain barrier with resulting protein secretion as a strategy for treatment of Niemann Picks type C2 disease

基因治疗血脑屏障并导致蛋白质分泌作为治疗尼曼匹克 C2 型疾病的策略

Eva Hede, Christine B Christiansen, Christian W Heegaard, Torben Moos, Annette Burkhart

The blood-brain barrier studied in vitro across species

跨物种体外血脑屏障研究

Maj Schneider Thomsen, Nanna Humle, Eva Hede, Torben Moos, Annette Burkhart, Louiza Bohn Thomsen