日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A phase 1 study of durvalumab as monotherapy or combined with tremelimumab with or without azacitidine in patients with myelodysplastic syndrome

一项针对骨髓增生异常综合征患者的1期研究,评估度伐利尤单抗单药治疗或联合曲美利木单抗(加或不加阿扎胞苷)的疗效。

Garcia-Manero, Guillermo; Gaddh, Manila; Platzbecker, Uwe; Lindsley, R Coleman; Larson, Sarah M; Chevassut, Timothy; Fenaux, Pierre; Komrokji, Rami; Lyons, Roger; Al-Kali, Aref; Jiang, Yu; Bothos, John; Townsley, Danielle M; Zeidan, Amer M

Efficacy and safety of acalabrutinib with best supportive care versus best supportive care in patients with COVID-19 requiring hospitalization

在需要住院治疗的 COVID-19 患者中,acalabrutinib 联合最佳支持治疗与单纯最佳支持治疗的疗效和安全性比较

Scheinberg, Phillip; Khoshnevis, Matt R; Robinson, Philip A; Guerreros, Alfredo; Sato, Victor A H; Fonseca, Benedito A L; Prozesky, Hans W; Romero, José Omar Chacón; Fogliatto, Laura; Meisenberg, Barry R; Park, David J; Gupta, Ashok; Patel, Priti; Townsley, Danielle M; Zheng, Lianqing; Munugalavadla, Veerendra

A unified metric of human immune health

人类免疫健康的统一指标

Sparks, Rachel; Rachmaninoff, Nicholas; Lau, William W; Hirsch, Dylan C; Bansal, Neha; Martins, Andrew J; Chen, Jinguo; Liu, Candace C; Cheung, Foo; Failla, Laura E; Biancotto, Angelique; Fantoni, Giovanna; Sellers, Brian A; Chawla, Daniel G; Howe, Katherine N; Mostaghimi, Darius; Farmer, Rohit; Kotliarov, Yuri; Calvo, Katherine R; Palmer, Cindy; Daub, Janine; Foruraghi, Ladan; Kreuzburg, Samantha; Treat, Jennifer D; Urban, Amanda K; Jones, Anne; Romeo, Tina; Deuitch, Natalie T; Moura, Natalia Sampaio; Weinstein, Barbara; Moir, Susan; Ferrucci, Luigi; Barron, Karyl S; Aksentijevich, Ivona; Kleinstein, Steven H; Townsley, Danielle M; Young, Neal S; Frischmeyer-Guerrerio, Pamela A; Uzel, Gulbu; Pinto-Patarroyo, Gineth Paola; Cudrici, Cornelia D; Hoffmann, Patrycja; Stone, Deborah L; Ombrello, Amanda K; Freeman, Alexandra F; Zerbe, Christa S; Kastner, Daniel L; Holland, Steven M; Tsang, John S

ASCT2-Targeting Antibody-Drug Conjugate MEDI7247 in Adult Patients with Relapsed/Refractory Hematological Malignancies: A First-in-Human, Phase 1 Study

ASCT2靶向抗体药物偶联物MEDI7247治疗复发/难治性血液系统恶性肿瘤成人患者:一项首次人体I期研究

Maris, Michael; Salles, Gilles; Kim, Won Seog; Kim, Tae Min; Lyons, Roger M; Arellano, Martha; Karmali, Reem; Schiller, Gary; Cull, Elizabeth; Abboud, Camille N; Batlevi, Connie; Kagiampakis, Ioannis; Rebelatto, Marlon C; Lee, Young; Kirby, Lyndon C; Wang, Fujun; Bothos, John; Townsley, Danielle M; Fathi, Amir T; Ribrag, Vincent

Multiomics integration of 22 immune-mediated monogenic diseases reveals an emergent axis of human immune health

对22种免疫介导的单基因疾病进行多组学整合,揭示了人类免疫健康的新兴轴心

Sparks, Rachel; Rachmaninoff, Nicholas; Hirsch, Dylan C; Bansal, Neha; Lau, William W; Martins, Andrew J; Chen, Jinguo; Liu, Candace C; Cheung, Foo; Failla, Laura E; Biancotto, Angelique; Fantoni, Giovanna; Sellers, Brian A; Chawla, Daniel G; Howe, Katherine N; Mostaghimi, Darius; Farmer, Rohit; Kotliarov, Yuri; Calvo, Katherine R; Palmer, Cindy; Daub, Janine; Foruraghi, Ladan; Kreuzburg, Samantha; Treat, Jennifer; Urban, Amanda K; Jones, Anne; Romeo, Tina; Deuitch, Natalie T; Moura, Natalia Sampaio; Weinstein, Barbara; Moir, Susan; Ferrucci, Luigi; Barron, Karyl S; Aksentijevich, Ivona; Kleinstein, Steven H; Townsley, Danielle M; Young, Neal S; Frischmeyer-Guerrerio, Pamela A; Uzel, Gulbu; Pinto-Patarroyo, Gineth Paola; Cudrici, Cornelia D; Hoffmann, Patrycja; Stone, Deborah L; Ombrello, Amanda K; Freeman, Alexandra F; Zerbe, Christa S; Kastner, Daniel L; Holland, Steven M; Tsang, John S

Eltrombopag added to immunosuppression for children with treatment-naïve severe aplastic anaemia

在对未经治疗的重型再生障碍性贫血患儿进行免疫抑制治疗时,可加入艾曲波帕。

Groarke, Emma M; Patel, Bhavisha A; Gutierrez-Rodrigues, Fernanda; Rios, Olga; Lotter, Jennifer; Baldoni, Daniela; St Pierre, Annie; Shalhoub, Ruba; Wu, Colin O; Townsley, Danielle M; Young, Neal S

Eltrombopag monotherapy can improve hematopoiesis in patients with low to intermediate risk-1 myelodysplastic syndrome

艾曲波帕单药治疗可改善低危至中危-1型骨髓增生异常综合征患者的造血功能。

Vicente, Alana; Patel, Bhavisha A; Gutierrez-Rodrigues, Fernanda; Groarke, Emma; Giudice, Valentina; Lotter, Jennifer; Feng, Xingmin; Kajigaya, Sachiko; Weinstein, Barbara; Barranta, Evette; Olnes, Matthew J; Parikh, Ankur R; Albitar, Maher; Wu, Colin O; Shalhoub, Ruba; Calvo, Katherine R; Townsley, Danielle M; Scheinberg, Phillip; Dunbar, Cynthia E; Young, Neal S; Winkler, Thomas

Eltrombopag for patients with moderate aplastic anemia or uni-lineage cytopenias

艾曲波帕用于治疗中度再生障碍性贫血或单系血细胞减少症患者

Fan, Xing; Desmond, Ronan; Winkler, Thomas; Young, David J; Dumitriu, Bogdan; Townsley, Danielle M; Gutierrez-Rodrigues, Fernanda; Lotter, Jennifer; Valdez, Janet; Sellers, Stephanie E; Barranta, Ma Evette; Shalhoub, Ruba N; Wu, Colin O; Albitar, Maher; Calvo, Katherine R; Young, Neal S; Dunbar, Cynthia E

The Spectrum of Hepatic Involvement in Patients With Telomere Disease

端粒病患者肝脏受累谱

Kapuria, Devika; Ben-Yakov, Gil; Ortolano, Rebecca; Cho, Min Ho; Kalchiem-Dekel, Or; Takyar, Varun; Lingala, Shilpa; Gara, Naveen; Tana, Michele; Kim, Yun Ju; Kleiner, David E; Young, Neal S; Townsley, Danielle M; Koh, Christopher; Heller, Theo

MDS-associated mutations in germline GATA2 mutated patients with hematologic manifestations

携带生殖系GATA2突变且伴有血液学表现的MDS相关突变

McReynolds, Lisa J; Yang, Yanqin; Yuen Wong, Hong; Tang, Jingrong; Zhang, Yubo; Mulé, Matthew P; Daub, Janine; Palmer, Cindy; Foruraghi, Ladan; Liu, Qingguo; Zhu, Jun; Wang, Weixin; West, Robert R; Yohe, Marielle E; Hsu, Amy P; Hickstein, Dennis D; Townsley, Danielle M; Holland, Steven M; Calvo, Katherine R; Hourigan, Christopher S