Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophy
利司他林治疗并未导致脊髓性肌萎缩症患者出现视网膜毒性。
期刊:Annals of Clinical and Translational Neurology
影响因子:3.9
doi:10.1002/acn3.51239
Sergott, Robert C; Amorelli, Giulia M; Baranello, Giovanni; Barreau, Emmanuel; Beres, Shannon; Kane, Steven; Mercuri, Eugenio; Orazi, Lorenzo; SantaMaria, Melissa; Tremolada, Gemma; Santarsiero, Diletta; Waskowska, Agnieszka; Yashiro, Shigeko; Denk, Nora; Fürst-Recktenwald, Sabine; Gerber, Marianne; Gorni, Ksenija; Jaber, Birgit; Jacobsen, Bjoern; Mueller, Lutz; Nave, Stephane; Scalco, Renata S; Marzoli, Stefania B