日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Deferiprone in Alzheimer Disease: A Randomized Clinical Trial

去铁酮治疗阿尔茨海默病:一项随机临床试验

Ayton, Scott; Barton, David; Brew, Bruce; Brodtmann, Amy; Clarnette, Roger; Desmond, Patricia; Devos, David; Ellis, Kathryn A; Fazlollahi, Amir; Fradette, Caroline; Goh, Anita M Y; Kalinowski, Pawel; Kyndt, Christopher; Lai, Rosalyn; Lim, Yen Ying; Maruff, Paul; O'Brien, Terence J; Rowe, Christopher; Salvado, Olivier; Schofield, Peter W; Spino, Michael; Tricta, Fernando; Wagen, Aaron; Williams, Robert; Woodward, Michael; Bush, Ashley I

Extramedullary haematopoiesis in patients with thalassemia: a cross-sectional description of its prevalence, clinical features and survival

地中海贫血患者髓外造血:其患病率、临床特征和生存率的横断面描述

Chapchap, Eduardo Cerello; Silva, Murilo Marques Almeida; Baroni, Ronaldo Hueb; Araujo, Aderson da Silva; de Assis, Reijane Alves; Loggetto, Sandra Regina; Junior, Antonio Fabron; Verissimo, Monica Pinheiro de Almeida; Baldanzi, Giorgio Roberto; Fertrin, Kleber Yotsumoto; Tricta, Fernando; Piga, Antonio Giulio; Hamerschlak, Nelson

Cardiac iron overload evaluation in thalassaemic patients using T2* magnetic resonance imaging following chelation therapy: a multicentre cross-sectional study

利用T2*磁共振成像评估地中海贫血患者螯合治疗后的心脏铁过载情况:一项多中心横断面研究

Chapchap, Eduardo Cerello; Silva, Murilo Marques Almeida; de Assis, Reijane Alves; Kerbauy, Lucila Nassif; Diniz, Michelli da Silva; Rosemberg, Laércio Alberto; Loggetto, Sandra Regina; Araujo, Aderson da Silva; Fabron Junior, Antonio; Verissimo, Monica Pinheiro de Almeida; Baldanzi, Giorgio Roberto; Esposito, Breno Pannia; Tricta, Fernando; Steagall, Merula Emmanoel Anargyrou; Vellozo, Claudia Ângela Galleni Di Sessa; Fertrin, Kleber Yotsumoto; Baroni, Ronaldo Hueb; Hamerschlak, Nelson

S122: SAFETY AND EFFICACY OF CRIZANLIZUMAB IN ADOLESCENTS WITH SICKLE CELL DISEASE (SCD): INITIAL DATA FROM THE PHASE II, MULTICENTER, OPEN-LABEL SOLACE-KIDS TRIAL

S122:克立珠单抗治疗镰状细胞病(SCD)青少年患者的安全性和有效性:来自 II 期多中心开放标签 Solace-Kids 试验的初步数据

van de Loosdrecht, Arjan A; Mandac Smoljanović, Inga; Adlette Inati, A; Maha Sabbagh, M; Chadi Al Alam, C; Ammar Al Kheir, A; Ziad Massouh, Z; Rawan Demachkie, R; Cristel Ojaimy, C; Nidhi Dani, N; Asif Siddiqui, A; Rishi Rajat Adhikary, R; Brendan Lynch, B; Abhishek Srivastava, A; Delaporta, P; Kyriakopoulou, D; Ioakeimidou, N; Solomou, E; Binenbaum, I; Toutoudaki, K; Chatzielefteriou, M; Papassotiriou, I; Kattamis, A; Dimopoulou, M; Komninaka, V; Flevari, P; Bartzi, V; Repa, K; Voskaridou, E; Badat, M; Hua, P; Mettananda, S; Fisher, C; Roy, N; Rice, S; Roy, A; Higgs, D; Davies, J; Elalfy, M; El-Beshlawy, A; Adly, A; Ebeid, F; Fradette, C; Lee, D; Temin, N; Tricta, F; Rozova, A; Hamdy, M; Giannaki, A; Fortis, S; Georgatzakou, H; Xidaki, A; Liosi, M; Fountzoula, C; Papageorgiou, E; Antonelou, M; Delicou, S; Kriebardis, A; Mayer, C; Cooper, D; Redfern, A; Geng, X; Shi, J; Zutphen-van Geffen, M; Kuan, I; Koek, K; Kastrissios, H; Patel, K; Davis, M; Yue, P; Callaghan, M; Ataga, K; De Franceschi, L; Minniti, C; Balachandran, N; Imbs, D; Perretti, T; Ramos, J; Sostelly, A; Bartolucci, P; Lal, A; Brown, C; Coates, T; Kalfa, T; Kwiatkowski, JL; Brevard, J; Trenor, C; Wood, K; Sheth, S; Heeney, M; Rees, D; de Montalembert, M; Odame, I; Brown, C; Wali, Y; Nguyen, T; Lam, D; Pfender, N; Kanter, J

The safety and acceptability of twice-daily deferiprone for transfusional iron overload: A multicentre, open-label, phase 2 study

每日两次服用去铁酮治疗输血性铁过载的安全性和可接受性:一项多中心、开放标签的 II 期研究

Badawy, Sherif M; Kattamis, Antonis; Ezzat, Hatoon; Deschamps, Benoît; Sicard, Eric; Fradette, Caroline; Zhao, Feng; Tricta, Fernando; Chung Tsang, Yu; Sheth, Sujit; Piga, Antonio

The pharmacokinetic and safety profile of single-dose deferiprone in subjects with sickle cell disease

单剂量去铁酮在镰状细胞病患者中的药代动力学和安全性特征

Soulières, Denis; Mercier-Ross, Jules; Fradette, Caroline; Rozova, Anna; Tsang, Yu Chung; Tricta, Fernando

Brain iron chelation by deferiprone in a phase 2 randomised double-blinded placebo controlled clinical trial in Parkinson's disease

一项针对帕金森病患者的2期随机双盲安慰剂对照临床试验,研究了去铁酮螯合脑铁的疗效

Martin-Bastida, Antonio; Ward, Roberta J; Newbould, Rexford; Piccini, Paola; Sharp, David; Kabba, Christina; Patel, Maneesh C; Spino, Michael; Connelly, John; Tricta, Fernando; Crichton, Robert R; Dexter, David T

Deferiprone-induced agranulocytosis: 20 years of clinical observations

去铁酮诱发的粒细胞缺乏症:20 年的临床观察

Tricta, Fernando; Uetrecht, Jack; Galanello, Renzo; Connelly, John; Rozova, Anna; Spino, Michael; Palmblad, Jan

Effects of renal impairment on the pharmacokinetics of orally administered deferiprone

肾功能损害对口服去铁酮药代动力学的影响

Fradette, Caroline; Pichette, Vincent; Sicard, Éric; Stilman, Anne; Jayashankar, Shalini; Tsang, Yu Chung; Spino, Michael; Tricta, Fernando

Cost-utility analysis of deferiprone for the treatment of β-thalassaemia patients with chronic iron overload: a UK perspective

去铁酮治疗慢性铁过载β-地中海贫血患者的成本效益分析:英国视角

Bentley, Anthony; Gillard, Samantha; Spino, Michael; Connelly, John; Tricta, Fernando