日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Common Threads in Pediatric Inflammatory Diseases: Insight Into Personalized Medicine

儿童炎症性疾病的共同特征:个性化医疗的启示

Patel, Trusha T; Conrad, Maire A; Kelsen, Judith R

Non-depleting anti-CD4 monoclonal antibody induces immune tolerance to ERT in a murine model of Pompe disease

非耗竭性抗CD4单克隆抗体在庞贝病小鼠模型中诱导对酶替代疗法的免疫耐受

Sun, Baodong; Banugaria, Suhrad G; Prater, Sean N; Patel, Trusha T; Fredrickson, Keri; Ringler, Douglas J; de Fougerolles, Antonin; Rosenberg, Amy S; Waldmann, Herman; Kishnani, Priya S

Algorithm for the early diagnosis and treatment of patients with cross reactive immunologic material-negative classic infantile pompe disease: a step towards improving the efficacy of ERT

针对交叉反应性免疫物质阴性的经典型婴儿庞贝病患者,制定早期诊断和治疗算法:提高酶替代疗法疗效的一步。

Banugaria, Suhrad G; Prater, Sean N; Patel, Trusha T; Dearmey, Stephanie M; Milleson, Christie; Sheets, Kathryn B; Bali, Deeksha S; Rehder, Catherine W; Raiman, Julian A J; Wang, Raymond A; Labarthe, Francois; Charrow, Joel; Harmatz, Paul; Chakraborty, Pranesh; Rosenberg, Amy S; Kishnani, Priya S

Skeletal muscle pathology of infantile Pompe disease during long-term enzyme replacement therapy

婴儿型庞贝病长期酶替代疗法期间的骨骼肌病理

Prater, Sean N; Patel, Trusha T; Buckley, Anne F; Mandel, Hanna; Vlodavski, Eugene; Banugaria, Suhrad G; Feeney, Erin J; Raben, Nina; Kishnani, Priya S

Persistence of high sustained antibodies to enzyme replacement therapy despite extensive immunomodulatory therapy in an infant with Pompe disease: need for agents to target antibody-secreting plasma cells

一名患有庞贝病的婴儿尽管接受了广泛的免疫调节治疗,但酶替代疗法仍持续存在高水平的抗体:需要靶向抗体分泌浆细胞的药物

Banugaria, Suhrad G; Patel, Trusha T; Mackey, Joanne; Das, Stuti; Amalfitano, Andrea; Rosenberg, Amy S; Charrow, Joel; Chen, Y-T; Kishnani, Priya S