Identification of small molecule and genetic modulators of AON-induced dystrophin exon skipping by high-throughput screening
利用高通量筛选鉴定AON诱导的肌营养不良蛋白外显子跳跃的小分子和基因调节剂
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0008348
O'Leary, Debra A; Sharif, Orzala; Anderson, Paul; Tu, Buu; Welch, Genevieve; Zhou, Yingyao; Caldwell, Jeremy S; Engels, Ingo H; Brinker, Achim