Tween 85-Modified Low Molecular Weight PEI Enhances Exon-Skipping of Antisense Morpholino Oligomer In Vitro and in mdx Mice
Tween 85修饰的低分子量PEI增强反义吗啉代寡核苷酸在体外和mdx小鼠体内的外显子跳跃
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2017.09.006
Wang, Mingxing; Wu, Bo; Tucker, Jason D; Shah, Sapana N; Lu, Peijuan; Bollinger, Lauren E; Lu, Qilong