In vivo expansion of gene-targeted hepatocytes through transient inhibition of an essential gene
通过暂时抑制必需基因实现基因靶向肝细胞的体内扩增
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doi:10.1101/2023.07.26.550728
Marco De Giorgi, So Hyun Park, Adam Castoreno, Mingming Cao, Ayrea Hurley, Lavanya Saxena, Marcel A Chuecos, Christopher J Walkey, Alexandria M Doerfler, Mia N Furgurson, M Cecilia Ljungberg, Kalyani R Patel, Sarah Hyde, Tyler Chickering, Stephanie Lefebvre, Kelly Wassarman, Patrick Miller, June Qin