日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

RNAi-mediated rheostat for dynamic control of AAV-delivered transgenes

RNAi 介导的变阻器用于动态控制 AAV 传递的转基因

Megha Subramanian, James McIninch, Ivan Zlatev, Mark K Schlegel, Charalambos Kaittanis, Tuyen Nguyen, Saket Agarwal, Timothy Racie, Martha Arbaiza Alvarado, Kelly Wassarman, Thomas S Collins, Tyler Chickering, Christopher R Brown, Karyn Schmidt, Adam B Castoreno, Svetlana Shulga-Morskaya, Elena Stam

In vivo expansion of gene-targeted hepatocytes through transient inhibition of an essential gene

通过暂时抑制必需基因实现基因靶向肝细胞的体内扩增

Marco De Giorgi, So Hyun Park, Adam Castoreno, Mingming Cao, Ayrea Hurley, Lavanya Saxena, Marcel A Chuecos, Christopher J Walkey, Alexandria M Doerfler, Mia N Furgurson, M Cecilia Ljungberg, Kalyani R Patel, Sarah Hyde, Tyler Chickering, Stephanie Lefebvre, Kelly Wassarman, Patrick Miller, June Qin

Synthesis, chirality-dependent conformational and biological properties of siRNAs containing 5'-(R)- and 5'-(S)-C-methyl-guanosine

含 5'-(R)- 和 5'-(S)-C-甲基鸟苷的 siRNA 的合成、手性依赖性构象和生物学特性

Atsushi Mikami, Namrata Erande, Shigeo Matsuda, Alexander Kel'in, Lauren Blair Woods, Tyler Chickering, Pradeep S Pallan, Mark K Schlegel, Ivan Zlatev, Martin Egli, Muthiah Manoharan