日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lentiviral Gene Therapy for Artemis-Deficient SCID

慢病毒基因疗法治疗Artemis缺陷型重症联合免疫缺陷症

Morton J Cowan,Jason Yu,Janelle Facchino,Carol Fraser-Browne,Ukina Sanford,Misako Kawahara,Jasmeen Dara,Janel Long-Boyle,Jess Oh,Wendy Chan,Shivali Chag,Lori Broderick,Deepak Chellapandian,Hélène Decaluwe,Catherine Golski,Diana Hu,Caroline Y Kuo,Holly K Miller,Aleksandra Petrovic,Robert Currier,Joan F Hilton,Divya Punwani,Christopher C Dvorak,Harry L Malech,R Scott McIvor,Jennifer M Puck

Lentivirus Mediated Correction of Artemis-Deficient Severe Combined Immunodeficiency

慢病毒介导的Artemis缺陷型重症联合免疫缺陷的纠正

Punwani, Divya; Kawahara, Misako; Yu, Jason; Sanford, Ukina; Roy, Sushmita; Patel, Kiran; Carbonaro, Denise A; Karlen, Andrea D; Khan, Sara; Cornetta, Kenneth; Rothe, Michael; Schambach, Axel; Kohn, Donald B; Malech, Harry L; McIvor, R Scott; Puck, Jennifer M; Cowan, Morton J

Strain background modifies phenotypes in the ATP8B1-deficient mouse

品系背景会影响ATP8B1缺陷小鼠的表型。

Shah, Sohela; Sanford, Ukina R; Vargas, Julie C; Xu, Hongmei; Groen, Annamiek; Paulusma, Coen C; Grenert, James P; Pawlikowska, Ludmila; Sen, Saunak; Elferink, Ronald P J Oude; Bull, Laura N