日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Targeting of Human Mitochondrial DNA with Programmable pAgo Nuclease

利用可编程pAgo核酸酶靶向人类线粒体DNA

Rimskaya, Beatrisa; Kropocheva, Ekaterina; Shchukina, Elza; Ulashchik, Egor; Gelfenbein, Daria; Lisitskaya, Lidiya; Shmanai, Vadim; Smirnikhina, Svetlana; Kulbachinskiy, Andrey; Mazunin, Ilya

Efficient target cleavage by Type V Cas12a effectors programmed with split CRISPR RNA

通过裂解 CRISPR RNA 编程的 V 型 Cas12a 效应子进行有效的靶向切割

Regina Shebanova, Natalia Nikitchina, Nikita Shebanov, Vladimir Mekler, Konstantin Kuznedelov, Egor Ulashchik, Ruslan Vasilev, Olga Sharko, Vadim Shmanai, Ivan Tarassov, Konstantin Severinov, Nina Entelis, Ilya Mazunin

Novel Cluster and Monomer-Based GalNAc Structures Induce Effective Uptake of siRNAs in Vitro and in Vivo

新型簇状和单体状 GalNAc 结构可诱导 siRNA 在体外和体内的有效吸收

Sharma, Vivek K; Osborn, Maire F; Hassler, Matthew R; Echeverria, Dimas; Ly, Socheata; Ulashchik, Egor A; Martynenko-Makaev, Yury V; Shmanai, Vadim V; Zatsepin, Timofei S; Khvorova, Anastasia; Watts, Jonathan K