Novel Cluster and Monomer-Based GalNAc Structures Induce Effective Uptake of siRNAs in Vitro and in Vivo
新型簇状和单体状 GalNAc 结构可诱导 siRNA 在体外和体内的有效吸收
期刊:Bioconjugate Chemistry
影响因子:3.9
doi:10.1021/acs.bioconjchem.8b00365
Sharma, Vivek K; Osborn, Maire F; Hassler, Matthew R; Echeverria, Dimas; Ly, Socheata; Ulashchik, Egor A; Martynenko-Makaev, Yury V; Shmanai, Vadim V; Zatsepin, Timofei S; Khvorova, Anastasia; Watts, Jonathan K