日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Glucose-free/high-protein diet improves hepatomegaly and exercise intolerance in glycogen storage disease type III mice

无葡萄糖/高蛋白饮食可改善糖原贮积症III型小鼠的肝肿大和运动不耐受症状。

Pagliarani, Serena; Lucchiari, Sabrina; Ulzi, Gianna; Ripolone, Michela; Violano, Raffaella; Fortunato, Francesco; Bordoni, Andreina; Corti, Stefania; Moggio, Maurizio; Bresolin, Nereo; Comi, Giacomo P

Morpholino-mediated SOD1 reduction ameliorates an amyotrophic lateral sclerosis disease phenotype

吗啉代寡核苷酸介导的SOD1减少可改善肌萎缩侧索硬化症的疾病表型

Nizzardo, M; Simone, C; Rizzo, F; Ulzi, G; Ramirez, A; Rizzuti, M; Bordoni, A; Bucchia, M; Gatti, S; Bresolin, N; Comi, G P; Corti, S

Spinal muscular atrophy phenotype is ameliorated in human motor neurons by SMN increase via different novel RNA therapeutic approaches

通过不同的新型RNA治疗方法增加SMN蛋白,可以改善人类运动神经元中的脊髓性肌萎缩症表型。

Nizzardo, Monica; Simone, Chiara; Dametti, Sara; Salani, Sabrina; Ulzi, Gianna; Pagliarani, Serena; Rizzo, Federica; Frattini, Emanuele; Pagani, Franco; Bresolin, Nereo; Comi, Giacomo; Corti, Stefania