Genome editing-mediated knock-in of therapeutic genes ameliorates the disease phenotype in a model of hemophilia
基因组编辑介导的治疗基因敲入改善了血友病模型中的疾病表型
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2022.08.002
Jeong Hyeon Lee, Hye-Kyung Oh, Beom Seok Choi, Ho Hyeon Lee, Kyu Jun Lee, Un Gi Kim, Jina Lee, Hyerim Lee, Geon Seong Lee, Se Jun Ahn, Jeong Pil Han, Seokjoong Kim, Su Cheong Yeom, Dong Woo Song