日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease

利用患者特异性体内基因编辑技术治疗罕见遗传疾病

Musunuru, Kiran; Grandinette, Sarah A; Wang, Xiao; Hudson, Taylor R; Briseno, Kevin; Berry, Anne Marie; Hacker, Julia L; Hsu, Alvin; Silverstein, Rachel A; Hille, Logan T; Ogul, Aysel N; Robinson-Garvin, Nancy A; Small, Juliana C; McCague, Sarah; Burke, Samantha M; Wright, Christina M; Bick, Sarah; Indurthi, Venkata; Sharma, Shweta; Jepperson, Michael; Vakulskas, Christopher A; Collingwood, Michael; Keogh, Katie; Jacobi, Ashley; Sturgeon, Morgan; Brommel, Christian; Schmaljohn, Ellen; Kurgan, Gavin; Osborne, Thomas; Zhang, He; Kinney, Kyle; Rettig, Garrett; Barbosa, Christopher J; Semple, Sean C; Tam, Ying K; Lutz, Cathleen; George, Lindsey A; Kleinstiver, Benjamin P; Liu, David R; Ng, Kim; Kassim, Sadik H; Giannikopoulos, Petros; Alameh, Mohamad-Gabriel; Urnov, Fyodor D; Ahrens-Nicklas, Rebecca C

Advancing gene-editing platforms to improve the viability of rare-disease therapeutics: key insights from a 2024 Scientific Exchange hosted by ARM, ISCT, and Danaher

推进基因编辑平台以提高罕见病疗法的可行性:由ARM、ISCT和丹纳赫公司联合主办的2024年科学交流会的主要见解

Urnov, Fyodor; Kassim, Sadik; Musunuru, Kiran; Liu, David; Lee, Ann; Barrera, Luis; Stetkiewicz, Pam; Bruno, Julianne; Hewitt, Matthew; Lister, Troy; Malech, Harry; Gasch, Lindsay; Diver, Matt; Gertler, Nicholas; Grignon, Felix; Le, Audrey; Lehmicke, Michael; Almendro-Navarro, Vanessa; Lembong, Josephine

Antigen-Specific T Cell Receptor Discovery for Treating Progressive Multifocal Leukoencephalopathy

发现用于治疗进行性多灶性白质脑病的抗原特异性 T 细胞受体

Sasha Gupta, Tijana Martinov, Ashley Thelen, Megumi Sunahara, Shwetha Mureli, Angie Vazquez, Josiah Gerdts, Ravi Dandekar, Irene Cortese, Camille Fouassier, Elaine Schanzer, Fyodor D Urnov, Alexander Marson, Brian R Shy, Philip D Greenberg, Michael R Wilson

Imagine CRISPR cures

想象一下 CRISPR 疗法

Urnov, Fyodor D

Persistent repression of tau in the brain using engineered zinc finger protein transcription factors

利用工程化锌指蛋白转录因子持续抑制大脑中的tau蛋白

Susanne Wegmann ,Sarah L DeVos ,Bryan Zeitler ,Kimberly Marlen ,Rachel E Bennett ,Marta Perez-Rando ,Danny MacKenzie ,Qi Yu ,Caitlin Commins ,Riley N Bannon ,Bianca T Corjuc ,Alison Chase ,Lisa Diez ,Hoang-Oanh B Nguyen ,Sarah Hinkley ,Lei Zhang ,Alicia Goodwin ,Annemarie Ledeboer ,Stephen Lam ,Irina Ankoudinova ,Hung Tran ,Nicholas Scarlott ,Rainier Amora ,Richard Surosky ,Jeffrey C Miller ,Ashley B Robbins ,Edward J Rebar ,Fyodor D Urnov ,Michael C Holmes ,Amy M Pooler ,Brigit Riley ,H Steve Zhang ,Bradley T Hyman

Evidence generation and reproducibility in cell and gene therapy research: A call to action

细胞和基因治疗研究中的证据生成和可重复性:行动呼吁

Abou-El-Enein, Mohamed; Angelis, Aris; Appelbaum, Frederick R; Andrews, Nancy C; Bates, Susan E; Bierman, Arlene S; Brenner, Malcolm K; Cavazzana, Marina; Caligiuri, Michael A; Clevers, Hans; Cooke, Emer; Daley, George Q; Dzau, Victor J; Ellis, Lee M; Fineberg, Harvey V; Goldstein, Lawrence S B; Gottschalk, Stephen; Hamburg, Margaret A; Ingber, Donald E; Kohn, Donald B; Krainer, Adrian R; Maus, Marcela V; Marks, Peter; Mummery, Christine L; Pettigrew, Roderic I; Rutter, Joni L; Teichmann, Sarah A; Terzic, Andre; Urnov, Fyodor D; Williams, David A; Wolchok, Jedd D; Lawler, Mark; Turtle, Cameron J; Bauer, Gerhard; Ioannidis, John P A

LuNER: Multiplexed SARS-CoV-2 detection in clinical swab and wastewater samples

LuNER:临床拭子和废水样本中SARS-CoV-2的多重检测

Stahl, Elizabeth C; Gopez, Allan R; Tsuchida, Connor A; Fan, Vinson B; Moehle, Erica A; Witkowsky, Lea B; Hamilton, Jennifer R; Lin-Shiao, Enrique; McElroy, Matthew; McDevitt, Shana L; Ciling, Alison; Tsui, C Kimberly; Pestal, Kathleen; Gildea, Holly K; Keller, Amanda; Sylvain, Iman A; Williams, Clara; Hirsh, Ariana; Ehrenberg, Alexander J; Kantor, Rose; Metzger, Matthew; Nelson, Kara L; Urnov, Fyodor D; Ringeisen, Bradley R; Giannikopoulos, Petros; Doudna, Jennifer A

Call for Papers: Expanding the Scale and Scope of Therapeutic Gene Editing

征稿启事:扩大治疗性基因编辑的规模和范围

Kiem, Hans-Peter; Gaudelli, Nicole N; Urnov, Fyodor D; Frederickson, Robert M; Herzog, Roland W

SARS-Cov2 Clinical Diagnostics: Academic Scientists Take on the COVID-19 Pandemic

SARS-CoV-2临床诊断:学术科学家们应对COVID-19疫情

Urnov, Fyodor

Unveiling the Role of the Most Impactful Cardiovascular Risk Locus through Haplotype Editing

通过单倍型编辑揭示最具影响力的心血管风险位点的作用

Valentina Lo Sardo ,Pavel Chubukov ,William Ferguson ,Aditya Kumar ,Evan L Teng ,Michael Duran ,Lei Zhang ,Gregory Cost ,Adam J Engler ,Fyodor Urnov ,Eric J Topol ,Ali Torkamani ,Kristin K Baldwin