日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Height, weight, and body mass index trajectories and their correlation with functional outcome assessments in boys with Duchenne muscular dystrophy

杜氏肌营养不良症男孩的身高、体重和体质指数变化轨迹及其与功能结果评估的相关性

Schiava, Marianela; Dang, Utkarsh J; Wood, Claire; Wong, Sze Choong; Ward, Leanne M; Lofra, Robert Muni; Mayhew, Anna; Martens, William B; Gregory, Stephanie; Griggs, Robert C; Guglieri, Michela

Evaluation of a serum protein signature as monitoring biomarker for Duchenne Muscular Dystrophy in a long-term clinical trial with corticosteroids

在长期皮质类固醇临床试验中,评估血清蛋白特征作为杜氏肌营养不良症监测生物标志物的价值

Degan, Chiara; Tobin, Rebecca A; de Vries, Sharon I; Jiménez-Requena, Albert; Peco, Amela; Guglieri, Michela; Diaz-Manera, Jordi; van der Burgt, Yuri E M; Vlijmen, Bart J M; Hathout, Yetrib; Szigyarto, Cristina Al-Khalili; Dang, Utkarsh J; Tsonaka, Roula; Spitali, Pietro

Test-Retest Reliability of Motor Function and Myometry Outcomes From the Vamorolone Trials in Duchenne Muscular Dystrophy

杜氏肌营养不良症患者接受Vamorolone治疗后运动功能和肌电图结果的重测信度

Tobin, Rebecca A; Hoffman, Eric P; Johnson, Linda; James, Meredith K; Clemens, Paula R; Dang, Utkarsh J

Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial

Vamorolone 与安慰剂和泼尼松治疗杜氏肌营养不良症男孩的疗效和安全性:一项随机临床试验

Guglieri, Michela; Clemens, Paula R; Perlman, Seth J; Smith, Edward C; Horrocks, Iain; Finkel, Richard S; Mah, Jean K; Deconinck, Nicolas; Goemans, Nathalie; Haberlova, Jana; Straub, Volker; Mengle-Gaw, Laurel J; Schwartz, Benjamin D; Harper, Amy D; Shieh, Perry B; De Waele, Liesbeth; Castro, Diana; Yang, Michelle L; Ryan, Monique M; McDonald, Craig M; Tulinius, Mar; Webster, Richard; McMillan, Hugh J; Kuntz, Nancy L; Rao, Vashmi K; Baranello, Giovanni; Spinty, Stefan; Childs, Anne-Marie; Sbrocchi, Annie M; Selby, Kathryn A; Monduy, Migvis; Nevo, Yoram; Vilchez-Padilla, Juan J; Nascimento-Osorio, Andres; Niks, Erik H; de Groot, Imelda J M; Katsalouli, Marina; James, Meredith K; van den Anker, Johannes; Damsker, Jesse M; Ahmet, Alexandra; Ward, Leanne M; Jaros, Mark; Shale, Phil; Dang, Utkarsh J; Hoffman, Eric P

Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial

Vamorolone治疗杜氏肌营养不良症的疗效和安全性:一项为期30个月的非随机对照开放标签扩展试验

Mah, Jean K; Clemens, Paula R; Guglieri, Michela; Smith, Edward C; Finkel, Richard S; Tulinius, Mar; Nevo, Yoram; Ryan, Monique M; Webster, Richard; Castro, Diana; Kuntz, Nancy L; McDonald, Craig M; Damsker, Jesse M; Schwartz, Benjamin D; Mengle-Gaw, Laurel J; Jackowski, Stefan; Stimpson, Georgia; Ridout, Deborah A; Ayyar-Gupta, Vandana; Baranello, Giovanni; Manzur, Adnan Y; Muntoni, Francesco; Gordish-Dressman, Heather; Leinonen, Mika; Ward, Leanne M; Hoffman, Eric P; Dang, Utkarsh J

Optimization of DOTAP/chol Cationic Lipid Nanoparticles for mRNA, pDNA, and Oligonucleotide Delivery

优化DOTAP/胆固醇阳离子脂质纳米粒子用于mRNA、pDNA和寡核苷酸递送

Sun, Mengwei; Dang, Utkarsh J; Yuan, Yuhao; Psaras, Alexandra Maria; Osipitan, Ositomiwa; Brooks, Tracy A; Lu, Fake; Di Pasqua, Anthony J

Subjective Cognitive Complaints in Unaffected First-Degree Relatives of Schizophrenia Patients: Relation to Cognitive Performance, Psychotic Experiences, and Social Functioning

精神分裂症患者未受影响的一级亲属的主观认知障碍:与认知能力、精神病性体验和社会功能的关系

Baliga, Sachin P; Kedare, Jahnavi S; Mankar, Utkarsh J; Kamath, Ravindra M

Interrogation of Dystrophin and Dystroglycan Complex Protein Turnover After Exon Skipping Therapy

外显子跳跃疗法后肌营养不良蛋白和肌营养不良蛋白复合体蛋白质周转率的探讨

James S Novak, Rita Spathis, Utkarsh J Dang, Alyson A Fiorillo, Ravi Hindupur, Christopher B Tully, Davi A G Mázala, Emily Canessa, Kristy J Brown, Terence A Partridge, Yetrib Hathout, Kanneboyina Nagaraju

Comparison of Serum Pharmacodynamic Biomarkers in Prednisone-Versus Deflazacort-Treated Duchenne Muscular Dystrophy Boys

泼尼松治疗与地夫可特治疗杜氏肌营养不良症男孩血清药效学生物标志物的比较

Tawalbeh, Shefa; Samsel, Alison; Gordish-Dressman, Heather; Hathout, Yetrib; Investigators, Cinrg-Dnhs; Dang, Utkarsh J

Serum protein biomarkers for juvenile dermatomyositis: a pilot study

幼年皮肌炎血清蛋白生物标志物:一项初步研究

Tawalbeh, Shefa M; Marin, Wilfredo; Morgan, Gabrielle A; Dang, Utkarsh J; Hathout, Yetrib; Pachman, Lauren M