AAV gene therapy in companion dogs with severe hemophilia: Real-world long-term data on immunogenicity, efficacy, and quality of life
针对患有严重血友病的伴侣犬的AAV基因疗法:关于免疫原性、疗效和生活质量的真实世界长期数据
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2024.101205
Doshi, Bhavya S; Samelson-Jones, Benjamin J; Nichols, Timothy C; Merricks, Elizabeth P; Siner, Joshua L; French, Robert A; Lee, Ben J; Arruda, Valder R; Callan, Mary Beth