日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Expanded clinical, genetic, and biological spectrum of filaminopathies with hematological involvement

扩展了伴有血液系统受累的丝氨酸蛋白病的临床、遗传和生物学谱

Brillon, Charlotte; Poggi, Marjorie; Fiore, Mathieu; Goizet, Cyril; Bayart, Sophie; Daniel, Mélanie Y; Valentin, Jean-Baptiste; Hezard, Nathalie; Van Agthoven, Johannes; Sbarra, Véronique; Loosveld, Marie; Falaise, Céline; Alessi, Marie-Christine; Ibrahim-Kosta, Manal; Saultier, Paul

Impact of Systematic Joint Examination (Ultrasound, Functional and Physical) on Treatment Management Decisions in Patients With Haemophilia A in France: Final Data From the Prospective, Observational A-MOVE Study

系统性关节检查(超声、功能和体格检查)对法国A型血友病患者治疗管理决策的影响:前瞻性观察性A-MOVE研究的最终数据

Drillaud, Nicolas; Barbay, Virginie; Valentin, Jean Baptiste; Jailler, Romain; Lebreton, Aurélien; Pan-Petesch, Brigitte; Marie Castet, Sabine; Frotscher, Birgit; Frenzel, Laurent; Jousse-Joulin, Sandrine; Chambost, Hervé; Alenäs, Mikaela; Fusser, Markus; Gandossi, Corinne; Zidi, Meriem; Mahdout, Oussama; Repessé, Yohann

ORPHEE: A Real-World Study on rIX-FP Prophylaxis Use in Adolescent/Adult Patients With Hemophilia B

ORPHEE:一项关于rIX-FP预防性治疗在B型血友病青少年/成人患者中应用的真实世界研究

Volot, Fabienne; Castet, Sabine; Fournel, Alexandra; Frotscher, Birgit; Gillet, Benjamin; Desprez, Dominique; Tardy, Brigitte; Rauch, Antoine; Chamouni, Pierre; Biron-Andreani, Christine; Valentin, Jean-Baptiste; Harroche, Annie; Dargaud, Yesim; Petesch, Brigitte Pan; d'Oiron, Roseline; Berger, Claire; Reynes, Claire; Lauvray, Thomas; de Raucourt, Emmanuelle; Hassoun, Abel; Lebreton, Aurélien; Cussac, Vincent; Catovic, Hasan; Martin, Cédric; Guillet, Benoit

NuPOWER (Nuwiq for Perioperative management Of patients With haemophilia A on Emicizumab Regular prophylaxis): protocol for an open-label, single-arm, multicentre study

NuPOWER(Nuwiq 用于接受 Emicizumab 常规预防治疗的 A 型血友病患者的围手术期管理):一项开放标签、单臂、多中心研究方案

Srivastava, Alok; Kanny, Angela; Langer, Florian; Kubicek-Hofmann, Cornelia; Álvarez Román, María Teresa; Núñez Vázquez, Ramiro; Boban, Ana; Dejanova-Ilijevska, Violeta; Miljić, Predrag; Garcia, Jessica; Halimeh, Susan; Drillaud, Nicolas; Valentin, Jean-Baptiste; Mancuso, Maria Elisa; Castaman, Giancarlo; Santoro, Rita Carlotta; Lehtinen, Anna-Elina; Abraham, Aby; Hashimoto, Mariko; Knaub, Sigurd

Developing a pragmatic consensus procedure supporting the ICH S1B(R1) weight of evidence carcinogenicity assessment

制定一项务实的共识程序,以支持ICH S1B(R1)证据权重致癌性评估

Bassan, Arianna; Steigerwalt, Ronald; Keller, Douglas; Beilke, Lisa; Bradley, Paul M; Bringezu, Frank; Brock, William J; Burns-Naas, Leigh Ann; Chambers, Jon; Cross, Kevin; Dorato, Michael; Elespuru, Rosalie; Fuhrer, Douglas; Hall, Frances; Hartke, Jim; Jahnke, Gloria D; Kluxen, Felix M; McDuffie, Eric; Schmidt, Friedemann; Valentin, Jean-Pierre; Woolley, David; Zane, Doris; Myatt, Glenn J

An overview of drug-induced sodium channel blockade and changes in cardiac conduction: Implications for drug safety

药物诱导的钠通道阻滞及心脏传导改变概述:对药物安全性的影响

Chaudhary, Khuram W; Clancy, Colleen E; Yang, Pei-Chi; Pierson, Jennifer B; Goldin, Alan L; Koerner, John E; Wisialowski, Todd A; Valentin, Jean-Pierre; Imredy, John P; Lagrutta, Armando; Authier, Simon; Kleiman, Robert; Sager, Philip T; Hoffmann, Peter; Pugsley, Michael K

Collaborative science in action: A 20 year perspective from the Health and Environmental Sciences Institute (HESI) Cardiac Safety Committee

合作科学实践:来自健康与环境科学研究所(HESI)心脏安全委员会的20年回顾

Pierson, Jennifer B; Berridge, Brian; Blinova, Ksenia; Brooks, Marjory B; Eldridge, Sandy; O'Brien, Claire E; Pugsley, Michael K; Schultze, A Eric; Smith, Godfrey; Stockbridge, Norman; Valentin, Jean-Pierre; Vicente, Jose

The evolving role of investigative toxicology in the pharmaceutical industry

调查毒理学在制药行业中不断演变的角色

Pognan, Francois; Beilmann, Mario; Boonen, Harrie C M; Czich, Andreas; Dear, Gordon; Hewitt, Philip; Mow, Tomas; Oinonen, Teija; Roth, Adrian; Steger-Hartmann, Thomas; Valentin, Jean-Pierre; Van Goethem, Freddy; Weaver, Richard J; Newham, Peter

H syndrome mimicking Erdheim Chester disease: new entity and therapeutic perspectives

类似埃尔德海姆切斯特病的 H 综合征:新实体和治疗观点

Hippolyte Lequain, Mathieu Gerfaud-Valentin, Jean-François Emile, Yann-Gaël Gangloff, Guilaine Boursier, Christophe Deligny, Guillaume Le Guenno, Juliet Tantot, Julie Valantin, Lea Savey, Claude Bachmeyer, Yvan Jamilloux, Laurent Schaeffer, Pascal Leblanc, Pascal Sève

Controlling DNA nanodevices with light-switchable buffers

利用光控缓冲液控制DNA纳米器件

Périllat, Valentin Jean; Del Grosso, Erica; Berton, Cesare; Ricci, Francesco; Pezzato, Cristian