Rescuing compounds for Lesch-Nyhan disease identified using stem cell-based phenotypic screening
利用基于干细胞的表型筛选鉴定出治疗莱希-尼汉病的救援化合物
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.132094
Valentin Ruillier, Johana Tournois, Claire Boissart, Marie Lasbareilles, Gurvan Mahé, Laure Chatrousse, Michel Cailleret, Marc Peschanski, Alexandra Benchoua
