A splice-switching antisense oligonucleotide approach for pediatric genetic epilepsies
一种用于治疗儿童遗传性癫痫的剪接转换反义寡核苷酸方法
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影响因子:
doi:10.1101/2025.10.22.683934
Dame, Haley B; Kopalle, Hema; Miñana, Belen; Klaft, Zin; Fahey, Jaclyn B; McWatters, David C; Rao, Vama; Suresh, Rushil; Aigner, Stefan; Hammer, Michael F; Yuskaitis, Christopher J; Wong, Megan; Teaney, Nicole; Zhang, Crystal; Thompson, Mike; Lehner, Ben; Bennett, C Frank; Valcárcel, Juan; Yeo, Gene W; Burge, Christopher B; Dulla, Chris G; Oudin, Madeleine J