日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Phase 2b program with sonlicromanol in patients with mitochondrial disease due to m.3243A>G mutation

针对因 m.3243A>G 突变引起的线粒体疾病患者,开展了 sonlicromanol 的 IIb 期临床试验项目。

Smeitink, Jan; van Es, Just; Bosman, Brigitte; Janssen, Mirian C H; Klopstock, Thomas; Gorman, Grainne; Vissing, John; Ruiterkamp, Gerrit; Edgar, Chris J; Abbink, Evertine J; van Maanen, Rob; Pogoryelova, Oksana; Stendel, Claudia; Bischoff, Almut; Karin, Ivan; Munshi, Mahtab; Kümmel, Anne; Burgert, Lydia; Verhaak, Christianne; Renkema, Herma

BIO101 in Sarcopenic Seniors at Risk of Mobility Disability: Results of a Double-Blind Randomised Interventional Phase 2b Trial

BIO101 在有行动障碍风险的肌少症老年人中的应用:一项双盲随机干预性 2b 期试验的结果

Fielding, Roger A; Dao, Michael M; Cannon, Kevin; Desvarieux, Moise; Miller, Sam S; Gimness, Michael Paul; Brandon, Donald M; Villareal, Dennis T; Bruyere, Olivier; Bautmans, Ivan; Rickner, Kyle; Perry, Robert; Kritchevsky, Stephen B; Musi, Nicolas; Chehade, Joe M; Kirstein, Judith L; Gielen, Evelien; Pickrell, Paul; Dilda, Pierre; Lafont, Rene; Margalef, Carole; Rolland, Yves; Del Signore, Susanna; Mariani, Jean; Agus, Samuel; Tourette, Cendrine; Dioh, Waly; van Maanen, Rob; Veillet, Stanislas

Characterizing sarcopenia and sarcopenic obesity in patients aged 65 years and over, at risk of mobility disability: a multicenter observational trial (SARA-OBS).

对 65 岁及以上有行动障碍风险的患者进行肌少症和肌少症性肥胖症的特征分析:一项多中心观察性试验 (SARA-OBS)

Fielding Roger A, Rolland Yves, Bruyere Olivier, Desvarieux Moise, Donini Lorenzo M, Incalzi Raffaele Antonelli, Muscaritoli Maurizio, Tchalla Achille, Bonnefoy Marc, Rondanelli Mariangela, Van Maanen Rob, Mariani Jean, Margalef Carole, Del Signore Susanna, Tourette Cendrine, Dioh Waly, Veillet Stanislas

Efficacy of oral 20-hydroxyecdysone (BIO101), a MAS receptor activator, in adults with severe COVID-19 (COVA): a randomized, placebo-controlled, phase 2/3 trial

口服20-羟基蜕皮激素(BIO101,一种MAS受体激活剂)治疗重症COVID-19成人患者的疗效(COVA):一项随机、安慰剂对照的II/III期试验

Lobo, Suzana Margareth; Plantefève, Gaétan; Nair, Girish; Joaquim Cavalcante, Adilson; Franzin de Moraes, Nara; Nunes, Estevao; Barnum, Otis; Berdun Stadnik, Claudio Marcel; Lima, Maria Patelli; Lins, Muriel; Hajjar, Ludhmila Abrahao; Lipinski, Christopher; Islam, Shaheen; Ramos, Fabiano; Simon, Tiago; Martinot, Jean-Benoît; Guimard, Thomas; Desclaux, Arnaud; Lioger, Bertrand; Neuenschwander, Fernando Carvalho; DeSouza Paolino, Bruno; Amin, Alpesh; Acosta, Samuel Amil; Dilling, Daniel Forde; Cartagena, Edgardo; Snyder, Brian; Devaud, Edouard; Barreto Berselli Marinho, Ana Karolina; Tanni, Suzana; Milhomem Beato, Patricia Medeiros; De Wit, Stephan; Selvan, Vani; Gray, Jeffrey; Fernandez, Ricardo; Pourcher, Valérie; Maddox, Lee; Kay, Richard; Azbekyan, Anait; Chabane, Mounia; Tourette, Cendrine; Esmeraldino, Luis Everton; Dilda, Pierre J; Lafont, René; Mariani, Jean; Camelo, Serge; Rabut, Sandrine; Agus, Samuel; Veillet, Stanislas; Dioh, Waly; van Maanen, Rob; Morelot-Panzini, Capucine

Novel Potential Targets for Function-Promoting Therapies: Orphan Nuclear Receptors, Anti-inflammatory Drugs, Troponin Activators, Mas Receptor Agonists, and Urolithin A

新型潜在功能促进疗法靶点:孤儿核受体、抗炎药物、肌钙蛋白激活剂、Mas受体激动剂和尿石素A

Dioh, Waly; Narkar, Vihang; Singh, Anurag; Malik, Fady; Ferrucci, Luigi; Tourette, Cendrine; Mariani, Jean; van Maanen, Rob; Fielding, Roger A

A randomised placebo-controlled, double-blind phase II study to explore the safety, efficacy, and pharmacokinetics of sonlicromanol in children with genetically confirmed mitochondrial disease and motor symptoms ("KHENERGYC")

一项随机、安慰剂对照、双盲 II 期研究,旨在探索 sonlicromanol 在基因确诊的线粒体疾病和运动症状儿童中的安全性、有效性和药代动力学(“KHENERGYC”)

Smeitink, Jan; van Maanen, Rob; de Boer, Lonneke; Ruiterkamp, Gerrit; Renkema, Herma

Community Consensus Guidelines to Support FAIR Data Standards in Clinical Research Studies in Primary Mitochondrial Disease

支持原发性线粒体疾病临床研究中 FAIR 数据标准的社区共识指南

Karaa, Amel; MacMullen, Laura E; Campbell, John C; Christodoulou, John; Cohen, Bruce H; Klopstock, Thomas; Koga, Yasutoshi; Lamperti, Costanza; van Maanen, Rob; McFarland, Robert; Parikh, Sumit; Rahman, Shamima; Scaglia, Fernando; Sherman, Alexander V; Yeske, Philip; Falk, Marni J

The use of mono- and combination drug therapy in men and women with lower urinary tract symptoms (LUTS) in the UK: a retrospective observational study

英国男性和女性下尿路症状(LUTS)患者单药及联合药物治疗的使用情况:一项回顾性观察研究

Ali, Mahmood; Landeira, Margarita; Covernton, Patrick J O; Choudhury, Nurul; Jaggi, Ashley; Fatoye, Francis; van Maanen, Rob

Safety and Efficacy of Fidaxomicin and Vancomycin in Children and Adolescents with Clostridioides (Clostridium) difficile Infection: A Phase 3, Multicenter, Randomized, Single-blind Clinical Trial (SUNSHINE)

菲达霉素和万古霉素治疗儿童和青少年艰难梭菌感染的安全性和有效性:一项 3 期多中心随机单盲临床试验 (SUNSHINE)

Wolf, Joshua; Kalocsai, Krisztina; Fortuny, Claudia; Lazar, Stefan; Bosis, Samantha; Korczowski, Bartosz; Petit, Arnaud; Bradford, Daniel; Croos-Dabrera, Rodney; Incera, Elodie; Melis, Joost; van Maanen, Rob

Long-term treatment of older patients with overactive bladder using a combination of mirabegron and solifenacin: a prespecified analysis from the randomized, phase III SYNERGY II study

使用米拉贝隆和索利那新联合治疗老年膀胱过度活动症患者的长期疗效:一项来自随机、III期SYNERGY II研究的预设分析

Mueller, Elizabeth R; van Maanen, Rob; Chapple, Christopher; Abrams, Paul; Herschorn, Sender; Robinson, Dudley; Stoelzel, Matthias; Yoon, Sang J; Al-Shukri, Salman; Rechberger, Tomasz; Gratzke, Christian