In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
利用体内慢病毒载体基因疗法治愈1型遗传性酪氨酸血症并预防癌前病变和癌变的发展
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-022-32576-7
Nicolas, Clara T; VanLith, Caitlin J; Hickey, Raymond D; Du, Zeji; Hillin, Lori G; Guthman, Rebekah M; Cao, William J; Haugo, Benjamin; Lillegard, Annika; Roy, Diya; Bhagwate, Aditya; O'Brien, Daniel; Kocher, Jean-Pierre; Kaiser, Robert A; Russell, Stephen J; Lillegard, Joseph B
