Ultrasound-mediated gene delivery specifically targets liver sinusoidal endothelial cells for sustained FVIII expression in hemophilia A mice.
超声介导的基因递送可特异性地靶向肝窦内皮细胞，从而在 A 型血友病小鼠中实现持续的 FVIII 表达
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.02.010
Lawton Savannah M, Manson Megan A, Fan Meng-Ni, Chao Ting-Yen, Chen Chun-Yu, Kim Peter, Campbell Carley, Cai Xiaohe, Vander Kooi Amber, Miao Carol H
