Spinal subpial delivery of AAV9 enables widespread gene silencing and blocks motoneuron degeneration in ALS
脊髓软膜下注射 AAV9 可实现广泛的基因沉默并阻止 ALS 中的运动神经元退化
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-019-0674-1
Mariana Bravo-Hernandez #, Takahiro Tadokoro #, Michael R Navarro, Oleksandr Platoshyn, Yoshiomi Kobayashi, Silvia Marsala, Atsushi Miyanohara, Stefan Juhas, Jana Juhasova, Helena Skalnikova, Zoltan Tomori, Ivo Vanicky, Hana Studenovska, Vladimir Proks, PeiXi Chen, Noe Govea-Perez, Dara Ditsworth, J