In Vivo Gene Editing of Muscle Stem Cells with Adeno-Associated Viral Vectors in a Mouse Model of Duchenne Muscular Dystrophy
在杜氏肌营养不良症小鼠模型中利用腺相关病毒载体对肌肉干细胞进行体内基因编辑
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2020.09.016
Jennifer B Kwon, Adarsh R Ettyreddy, Ashish Vankara, Joel D Bohning, Garth Devlin, Stephen D Hauschka, Aravind Asokan, Charles A Gersbach