Partial correction of cystinuria type A in mice via kidney-targeted transposon delivery.
通过肾脏靶向转座子递送部分纠正小鼠 A 型胱氨酸尿症
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2025.102639
Woodard Lauren E, Welch Richard C, Menshikh Anna, Luo Wentian, Williams Felisha M, Peek Jennifer L, Sha Feng, Veach Ruth Ann, Kaja Aparna, Beckerman Thomas M, Ikizler Talat Alp, Wilson Matthew H