Selumetinib in children with neurofibromatosis type 1 and asymptomatic inoperable plexiform neurofibroma at risk for developing tumor-related morbidity
Selumetinib 用于患有 1 型神经纤维瘤病和无症状不可手术的丛状神经纤维瘤且有发生肿瘤相关并发症风险的儿童
期刊:Neuro-Oncology
影响因子:13.4
doi:10.1093/neuonc/noac109
Gross, Andrea M; Glassberg, Brittany; Wolters, Pamela L; Dombi, Eva; Baldwin, Andrea; Fisher, Michael J; Kim, AeRang; Bornhorst, Miriam; Weiss, Brian D; Blakeley, Jaishri O; Whitcomb, Patricia; Paul, Scott M; Steinberg, Seth M; Venzon, David J; Martin, Staci; Carbonell, Amanda; Heisey, Kara; Therrien, Janet; Kapustina, Oxana; Dufek, Anne; Derdak, Joanne; Smith, Malcolm A; Widemann, Brigitte C