日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Assessing Overall Survival Benefits in Advanced Cancers: The Role of External Comparator Cohort Studies with Real-World Data

评估晚期癌症患者的总体生存获益:基于真实世界数据的外部对照队列研究的作用

Pignatti, Francesco; El-Galaly, Tarec Christoffer; Kaiser, Martin; Porkka, Kimmo; Doeswijk, Robin; Mol, Peter; Rivera, Donna R; Lerro, Catherine C; Rohr, Ulrich-Peter; Verpillat, Patrice; Valachis, Antonios; Trapani, Dario; Di Maio, Massimo; Latino, Nicola; Cordoba, Raul; Cherny, Nathan; Koopman, Miriam; Martins-Branco, Diogo; Pentheroudakis, George; Postmus, Douwe

Clinical Evidence 2030

临床证据2030

Arlett, Peter; Umuhire, Denise; Verpillat, Patrice; Foggi, Paolo; Wändel Liminga, Ulla; Sepodes, Bruno; Lunzer, Marianne; Aylward, Brian; Vamvakas, Spiros; Roes, Kit; Pétavy, Frank; Thirstrup, Steffen; Lamas, Maria; Cooke, Emer; Broich, Karl

Optimizing Patient Registries for Regulatory Decision Making - Key Learnings From an HMA/EMA Multistakeholder Workshop

优化患者登记系统以辅助监管决策——HMA/EMA多方利益相关者研讨会的主要经验总结

Plueschke, Kelly; Jonker, Carla; Kankanen, Hanna; Vetter, Thorsten; Sepodes, Bruno; Naehrlich, Lutz; Hillert, Jan; Crane, Gracy; Straus, Sabine; Foggi, Paolo; Martin, Simona; Kyriakopoulou, Christina; Mol, Peter; Day, Francesca; Breen, Kieran; Bennett, Neil; de Lemus Belmonte, Mencia; Bennett, Simon; Verpillat, Patrice; Roes, Kit C B; Cochino, Ana; Schaefer, Franz; Hernández-Rivas, Jesús María; McGettigan, Patricia; Arlett, Peter

Collaborative Real-World Evidence Among Regulators: Lessons and Perspectives

监管机构间协作的真实世界证据:经验教训与展望

Beck, Andrew E; Kampman, Melissa; Huynh, Cindy; Simon, Craig; Plueschke, Kelly; Cohet, Catherine; Verpillat, Patrice; Robinson, Kelly; Arlett, Peter

Leveraging patient experience data to guide medicines development, regulation, access decisions and clinical care in the EU

利用患者体验数据指导欧盟的药品研发、监管、准入决策和临床护理

Almeida, Diogo; Umuhire, Denise; Gonzalez-Quevedo, Rosa; António, Ana; Burgos, Juan Garcia; Verpillat, Patrice; Bere, Nathalie; Sepodes, Bruno; Torre, Carla

Fetal Lung Volume Appears to Predict Respiratory Morbidity in Congenital Diaphragmatic Hernia

胎儿肺容量似乎可以预测先天性膈疝的呼吸系统疾病

Cerbelle, Valentine; Le Duc, Kévin; Lejeune, Stephanie; Mur, Sébastien; Lerisson, Héloise; Drumez, Elodie; Sfeir, Rony; Bigot, Julien; Verpillat, Pauline; Boukhris, Riadh; Vaast, Pascal; Mordacq, Clémence; Thumerelle, Caroline; Storme, Laurent; Deschildre, Antoine; Center For Rare Disease Congenital Diaphragmatic Hernia

Principles for Good Practice in the Conduct of Non-interventional Studies: The View of Industry Researchers

非干预性研究良好实践原则:行业研究人员的观点

Acha, Virginia; Barefoot, Bart; Juarez Garcia, Ariadna; Lehner, Valerie; Monno, Raffaella; Sandler, Susan; Spooner, Almath; Verpillat, Patrice

Multicenter External Validation of the Deep Pelvic Endometriosis Index Magnetic Resonance Imaging Score

深部盆腔子宫内膜异位症指数磁共振成像评分的多中心外部验证

Thomassin-Naggara, Isabelle; Monroc, Michele; Chauveau, Benoit; Fauconnier, Arnaud; Verpillat, Pauline; Dabi, Yohann; Gavrel, Marie; Bolze, Pierre-Adrien; Darai, Emile; Touboul, Cyril; Lamrabet, Samia; Collinet, Pierre; Zareski, Elise; Bourdel, Nicolas; Roman, Horace; Rousset, Pascal

Dosing Characteristics of Recombinant Human Luteinizing Hormone or Human Menopausal Gonadotrophin-Derived LH Activity in Patients Undergoing Ovarian Stimulation: A German Fertility Database Study

德国生育数据库研究:接受卵巢刺激治疗的患者中重组人黄体生成素或人绝经期促性腺激素衍生的LH活性的剂量特征

Strezsak, Valerie; Allignol, Arthur; Bühler, Klaus; Fischer, Robert; Hubbard, Julie; Longobardi, Salvatore; Lispi, Monica; Schertz, Joan; Verpillat, Patrice

Rare metabolic disease mimicking COL4A1/COL4A2 fetal brain phenotype

一种罕见的代谢性疾病,其表型与 COL4A1/COL4A2 胎儿脑表型相似

Coste, T; Aloui, C; Petit, F; Moutton, S; Devisme, L; Wells, C F; Leboucq, N; Verpillat, P; Yvert, M; Rivier, F; Tournier-Lasserve, E