Small molecule 1a reduces FMRpolyG-mediated toxicity in in vitro and in vivo models for FMR1 premutation.
小分子 1a 可降低 FMRpolyG 介导的 FMR1 前突变体外和体内模型的毒性
期刊:Human Molecular Genetics
影响因子:3.2
doi:10.1093/hmg/ddab143
Haify Saif N, Buijsen Ronald A M, Verwegen Lucas, Severijnen Lies-Anne W F M, de Boer Helen, Boumeester Valerie, Monshouwer Roos, Yang Wang-Yong, Cameron Michael D, Willemsen Rob, Disney Matthew D, Hukema Renate K
