mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapy
用于(表观)基因组编辑和基因治疗的 mRNA 反式剪接双 AAV 载体
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-023-42386-0
Lisa Maria Riedmayr, Klara Sonnie Hinrichsmeyer, Stefan Bernhard Thalhammer, David Manuel Mittas, Nina Karguth, Dina Yehia Otify, Sybille Böhm, Valentin Johannes Weber, Michael David Bartoschek, Victoria Splith, Manuela Brümmer, Raphael Ferreira, Nanda Boon, Gabriele Maria Wögenstein, Christian Grim