An in vitro and in vivo efficacy evaluation of gene therapy candidate SBT101 in mouse models of adrenomyeloneuropathy and in NHPs
基因治疗候选药物 SBT101 在肾上腺脊髓神经病变小鼠模型和 NHP 中的体外和体内疗效评估
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2024.101354
Vidyullatha Vasireddy, Casey A Maguire, David W Anderson, Carrie Ng, Yi Gong, Florian Eichler, Stéphane Fourcade, Cristina Guilera, Andrea Onieva, Angela Sanchez, Marc Leal-Julià, Sergi Verdés, Inge M E Dijkstra, Stephan Kemp, HongGeun Park, Tiffany Lutz, Sean W Clark, Assumpció Bosch, Aurora Pujol,