Acipimox in Mitochondrial Myopathy (AIMM): study protocol for a randomised, double-blinded, placebo-controlled, adaptive design trial of the efficacy of acipimox in adult patients with mitochondrial myopathy
阿昔莫司治疗线粒体肌病(AIMM):一项随机、双盲、安慰剂对照、适应性设计试验的研究方案,旨在评估阿昔莫司治疗成人线粒体肌病患者的疗效。
期刊:Trials
影响因子:2
doi:10.1186/s13063-022-06544-x
Abouhajar, Alaa; Alcock, Lisa; Bigirumurame, Theophile; Bradley, Penny; Brown, Laura; Campbell, Ian; Del Din, Silvia; Faitg, Julie; Falkous, Gavin; Gorman, Gráinne S; Lakey, Rachel; McFarland, Robert; Newman, Jane; Rochester, Lynn; Ryan, Vicky; Smith, Hesther; Steel, Alison; Stefanetti, Renae J; Su, Huizhong; Taylor, Robert W; Thomas, Naomi J P; Tuppen, Helen; Vincent, Amy E; Warren, Charlotte; Watson, Gillian