Gene therapy for Bietti crystalline corneoretinal dystrophy: A phase 1/2 clinical trial
基因疗法治疗比埃蒂晶状体性角膜视网膜营养不良:一项 1/2 期临床试验
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2026.01.005
Yang, Liping; Xing, Dongjun; Zhang, Jinlu; Liu, Boshi; Jiang, Xiaoshuang; Chen, Shaohong; Li, Wang; Qu, Baoyuan; Qiao, Jing; Feng, Xuefeng; Jia, Haicun; Hu, Xianjun; Yu, Shicheng; Jia, Ruixuan; Wang, Likun; Mahajan, Vinit B; Dou, Hongliang; Lu, Fang; Li, Xiaorong