Retinal organoids mirror CRISPR-Cas9 gene editing efficiency observed in vivo
视网膜类器官反映了体内观察到的 CRISPR-Cas9 基因编辑效率。
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101627
Pulman, Juliette; Malki, Hugo; Oudin, Paul; Aydin, Ecem; Tran, Sophie; Visticot, Laura; Robert, Camille; De Cian, Anne; As, Marie; Goureau, Olivier; Concordet, Jean-Paul; Dalkara, Deniz