日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Identification of highly selective SIK1/2 inhibitors that modulate innate immune activation and suppress intestinal inflammation

鉴定能够调节先天免疫激活并抑制肠道炎症的高选择性SIK1/2抑制剂

Babbe, Holger; Sundberg, Thomas B; Tichenor, Mark; Seierstad, Mark; Bacani, Genesis; Berstler, James; Chai, Wenying; Chang, Leon; Chung, De Michael; Coe, Kevin; Collins, Bernard; Finley, Michael; Guletsky, Alexander; Lemke, Christopher T; Mak, Puiying A; Mathur, Ashok; Mercado-Marin, Eduardo V; Metkar, Shailesh; Raymond, Donald D; Rives, Marie-Laure; Rizzolio, Michele; Shaffer, Paul L; Smith, Russell; Smith, Jacqueline; Steele, Ruth; Steffens, Helena; Suarez, Javier; Tian, Gaochao; Majewski, Nathan; Volak, Laurie P; Wei, Jianmei; Desai, Prerak T; Ong, Luvena L; Koudriakova, Tatiana; Goldberg, Steven D; Hirst, Gavin; Kaushik, Virendar K; Ort, Tatiana; Seth, Nilufer; Graham, Daniel B; Plevy, Scott; Venable, Jennifer D; Xavier, Ramnik J; Towne, Jennifer E

Real-Time Interference Artifacts Suppression in Array of ToF Sensors

实时干扰伪影抑制在飞行时间传感器阵列中的应用

Volak, Jozef; Bajzik, Jakub; Janisova, Silvia; Koniar, Dusan; Hargas, Libor

Gene therapy for Alzheimer's disease targeting CD33 reduces amyloid beta accumulation and neuroinflammation

针对 CD33 的阿尔茨海默病基因治疗可减少淀粉样蛋白 β 的积累和神经炎症

Ana Griciuc, Anthony N Federico, Jeyashree Natasan, Angela M Forte, Danielle McGinty, Huong Nguyen, Adrienn Volak, Stanley LeRoy, Sheetal Gandhi, Eli P Lerner, Eloise Hudry, Rudolph E Tanzi, Casey A Maguire

High levels of AAV vector integration into CRISPR-induced DNA breaks

AAV 载体高水平整合到 CRISPR 诱导的 DNA 断裂中

Killian S Hanlon, Benjamin P Kleinstiver, Sara P Garcia, Mikołaj P Zaborowski, Adrienn Volak, Stefan E Spirig, Alissa Muller, Alexander A Sousa, Shengdar Q Tsai, Niclas E Bengtsson, Camilla Lööv, Martin Ingelsson, Jeffrey S Chamberlain, David P Corey, Martin J Aryee, J Keith Joung, Xandra O Breakefi

Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human Primate

利用 AAV9-PHP.B 进行基因转移可挽救 Usher 综合征 3A 小鼠模型的听力,并转导非人灵长类动物的毛细胞。

György, Bence; Meijer, Elise J; Ivanchenko, Maryna V; Tenneson, Kelly; Emond, Frederick; Hanlon, Killian S; Indzhykulian, Artur A; Volak, Adrienn; Karavitaki, K Domenica; Tamvakologos, Panos I; Vezina, Mark; Berezovskii, Vladimir K; Born, Richard T; O'Brien, Maureen; Lafond, Jean-François; Arsenijevic, Yvan; Kenna, Margaret A; Maguire, Casey A; Corey, David P

Intrathecal Adeno-Associated Viral Vector-Mediated Gene Delivery for Adrenomyeloneuropathy

鞘内腺相关病毒载体介导的基因递送治疗肾上腺脊髓神经病

Yi Gong ,Anna Berenson ,Fiza Laheji ,Guangping Gao ,Dan Wang ,Carrie Ng ,Adrienn Volak ,Rene Kok ,Vasileios Kreouzis ,Inge M Dijkstra ,Stephan Kemp ,Casey A Maguire ,Florian Eichler

CRISPR/Cas9 Mediated Disruption of the Swedish APP Allele as a Therapeutic Approach for Early-Onset Alzheimer's Disease

CRISPR/Cas9 介导破坏瑞典 APP 等位基因作为治疗早发性阿尔茨海默病的一种方法

Bence György, Camilla Lööv, Mikołaj P Zaborowski, Shuko Takeda, Benjamin P Kleinstiver, Caitlin Commins, Ksenia Kastanenka, Dakai Mu, Adrienn Volak, Vilmantas Giedraitis, Lars Lannfelt, Casey A Maguire, J Keith Joung, Bradley T Hyman, Xandra O Breakefield, Martin Ingelsson

Efficient Gene Transfer to the Central Nervous System by Single-Stranded Anc80L65

利用单链Anc80L65高效基因转移至中枢神经系统

Hudry, Eloise; Andres-Mateos, Eva; Lerner, Eli P; Volak, Adrienn; Cohen, Olivia; Hyman, Bradley T; Maguire, Casey A; Vandenberghe, Luk H

Virus vector-mediated genetic modification of brain tumor stromal cells after intravenous delivery

静脉注射后病毒载体介导的脑肿瘤基质细胞基因修饰

Volak, Adrienn; LeRoy, Stanley G; Natasan, Jeya Shree; Park, David J; Cheah, Pike See; Maus, Andreas; Fitzpatrick, Zachary; Hudry, Eloise; Pinkham, Kelsey; Gandhi, Sheetal; Hyman, Bradley T; Mu, Dakai; GuhaSarkar, Dwijit; Stemmer-Rachamimov, Anat O; Sena-Esteves, Miguel; Badr, Christian E; Maguire, Casey A

Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV

使用外泌体相关 AAV 将基因传递至内耳毛细胞以挽救听力

Bence György, Cyrille Sage, Artur A Indzhykulian, Deborah I Scheffer, Alain R Brisson, Sisareuth Tan, Xudong Wu, Adrienn Volak, Dakai Mu, Panos I Tamvakologos, Yaqiao Li, Zachary Fitzpatrick, Maria Ericsson, Xandra O Breakefield, David P Corey, Casey A Maguire