日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

One Shock, Not One Cure: Electroporation Reveals Disease-Specific Constraints in Hepatocyte Gene Editing Therapy.

一次电击,而非一次治愈:电穿孔揭示肝细胞基因编辑疗法中疾病特异性限制

Clark Callie, Pokhrel Menam, Arthur Benjamin, Suresh Pramita, Ates Ilayda, Gibson Justin, Dhungana Abishek, Mehlem Ryan, Boysia Andrew, Padalkar Mugdha V, Pokhrel Achala, Echesabal-Chen Jing, Vonada Anne, Stamatikos Alexis, Savinova Olga V, Grompe Markus, Cottle Renee N

Coding-Sequence Evolution Does Not Explain Divergence in Petal Anthocyanin Pigmentation Between Mimulus luteus Var luteus and M. l. variegatus

编码序列进化无法解释黄花猴面花(Mimulus luteus var luteus)和杂色猴面花(M. l. variegatus)花瓣花青素色素的差异

Orr, Walker E; Kim, Ji Yang; Márquez, Iker J Sánchez; Ryan, Caine J; Raj, Tejas; Hom, Ellen K; Person, Ashley E; Vonada, Anne; Stratton, John A; Cooley, Arielle M

Complete correction of murine phenylketonuria by selection-enhanced hepatocyte transplantation

通过选择性增强肝细胞移植完全纠正小鼠苯丙酮尿症

Vonada, Anne; Wakefield, Leslie; Martinez, Michael; Harding, Cary O; Grompe, Markus; Tiyaboonchai, Amita

In vivo tracing of the Cytokeratin 14 lineages using self-cleaving guide RNAs and CRISPR/Cas9.

利用自切割向导 RNA 和 CRISPR/Cas9 对细胞角蛋白 14 谱系进行体内追踪

Tiyaboonchai Amita, Wakefield Leslie, Vonada Anne, May Catherine L, Dorrell Craig, Enicks David, Sairavi Anusha, Kaestner Klaus H, Grompe Markus