日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

SEED-Selection enables high-efficiency enrichment of primary T cells edited at multiple loci

SEED-Selection技术能够高效富集在多个位点编辑过的原代T细胞。

Chang, Christopher R; Vykunta, Vivasvan S; Lee, Jae Hyun J; Li, Ke; Kochendoerfer, Clara; Muldoon, Joseph J; Wang, Charlotte H; Mazumder, Thomas; Sun, Yang; Goodman, Daniel B; Nyberg, William A; Liu, Chang; Allain, Vincent; Rothrock, Allison; Ye, Chun J; Marson, Alexander; Shy, Brian R; Eyquem, Justin

Pathogenic UNC13A variants cause a neurodevelopmental syndrome by impairing synaptic function

致病性UNC13A变异体通过损害突触功能导致神经发育综合征。

Asadollahi, Reza; Ahmad, Aisha; Boonsawat, Paranchai; Shahanoor Hinzen, Jasmine; Lohse, Mareike; Bouazza-Arostegui, Boris; Sun, Siqi; Utesch, Tillmann; Sommer, Jonas D; Ilic, Dragana; Padmanarayana, Murugesh; Fischermanns, Kati; Ranjan, Mrinalini; Boll, Moritz; Ka, Chandran; Piton, Amélie; Mattioli, Francesca; Isidor, Bertrand; Õunap, Katrin; Reinson, Karit; Wojcik, Monica H; Marshall, Christian R; Mercimek-Andrews, Saadet; Matsumoto, Naomichi; Miyake, Noriko; Stephan, Bruno de Oliveira; Honjo, Rachel Sayuri; Bertola, Debora R; Kim, Chong Ae; Yusupov, Roman; Mefford, Heather C; Christodoulou, John; Lee, Joy; Heath, Oliver; Brown, Natasha J; Baker, Naomi; Stark, Zornitza; Delatycki, Martin; Lake, Nicole J; Zeidler, Shimriet; Zuurbier, Linda; Maas, Saskia M; de Kruiff, Chris C; Rajabi, Farrah; Rodan, Lance H; Coury, Stephanie A; Platzer, Konrad; Oppermann, Henry; Abou Jamra, Rami; Beblo, Skadi; Maxton, Caroline; Śmigiel, Robert; Underhill, Hunter; Dubbs, Holly; Rosen, Alyssa; Helbig, Katherine L; Helbig, Ingo; Ruggiero, Sarah McKeown; Fitzgerald, Mark P; Kraemer, Dennis; Prada, Carlos E; Tenney, Jeffrey; Jayakar, Parul; Redon, Sylvia; Lefranc, Jérémie; Uguen, Kevin; Race, Simone; Efthymiou, Stephanie; Maroofian, Reza; Houlden, Henry; Coppens, Sandra; Deconinck, Nicolas; Ashokkumar, Balasubramaniem; Varalakshmi, Perumal; Gowda K, Vykunta Raju; Eghbal, Fatemeh; Ghayoor Karimiani, Ehsan; Heidari, Morteza; Neidhardt, John; Owczarek-Lipska, Marta; Korenke, G Christoph; Bamshad, Michael J; Campeau, Philippe M; Lehman, Anna; Hendon, Laura G; Wentzensen, Ingrid M; Monaghan, Kristin G; Chen, Yanmin; Szuto, Anna; Cohn, Ronald D; Au, Ping Yee Billie; Hübner, Christoph; Boschann, Felix; Manickam, Kandamurugu; Koboldt, Daniel C; Rad, Aboulfazl; Oprea, Gabriela; Bachman, Kristine K; Seeley, Andrea H; Agolini, Emanuele; Terracciano, Alessandra; Carmelo, Piscopo; Bupp, Caleb; Grysko, Bethany; Rein-Rothschild, Annick; Ben Zeev, Bruria; Margolin, Amy; Morrison, Jennifer; Dagli, Aditi; Stolerman, Elliot; Louie, Raymond J; Washington, Camerun; Stevens, Servi J C; Heijligers, Malou; Alkuraya, Fowzan S; Lisfeld, Jasmin; Neu, Axel; Paoli Monteiro, Fabíola; Santos Pessoa, André Luiz; Camelo-Filho, Antonio Edvan; Kok, Fernando; Koeberl, Dwight; Riley, Kacie; Burglen, Lydie; Doummar, Diane; Héron, Bénédicte; Mignot, Cyril; Keren, Boris; Charles, Perrine; Nava, Caroline; Bernhard, Felix P; Kühn, Andrea A; Thoms, Sven; Morrie, Ryan D; Mekhoubad, Shila; Green, Eric M; Barmada, Sami J; Gitler, Aaron D; Jahn, Olaf; Rhee, Jeong Seop; Rosenmund, Christian; Mitkovski, Mišo; Sticht, Heinrich; Sun, Han; Le Gac, Gerald; Taschenberger, Holger; Brose, Nils; Dittman, Jeremy S; Rauch, Anita; Lipstein, Noa

Hybrid intelligent systems for liver disease prediction: a demographic-aware machine learning framework

用于肝病预测的混合智能系统:一种考虑人口统计信息的机器学习框架

Saraf, Ekta; Yang, Mao; Sakthivel, Ramalingam; Zhang, Yiquan; Chokkakula, Santosh; Kong, Yu; Alekya, Vykunta; Naveen, Bommireddy; Yang, Bing

Mast cells help organize the Peyer's patch niche for induction of IgA responses

肥大细胞有助于组织派氏淋巴集结的微环境,从而诱导IgA反应。

Marco De Giovanni ,Vivasvan S Vykunta ,Adi Biram ,Kevin Y Chen ,Hanna Taglinao ,Jinping An ,Dean Sheppard ,Helena Paidassi ,Jason G Cyster

Ultra-high efficiency T cell reprogramming at multiple loci with SEED-Selection

使用 SEED-Selection 在多个基因座进行超高效 T 细胞重编程

Christopher R Chang, Vivasvan S Vykunta, Daniel B Goodman, Joseph J Muldoon, William A Nyberg, Chang Liu, Vincent Allain, Allison Rothrock, Charlotte H Wang, Alexander Marson, Brian R Shy, Justin Eyquem

High-yield genome engineering in primary cells using a hybrid ssDNA repair template and small-molecule cocktails

使用混合 ssDNA 修复模板和小分子混合物在原代细胞中进行高产基因组工程

Brian R Shy #, Vivasvan S Vykunta #, Alvin Ha, Alexis Talbot, Theodore L Roth, David N Nguyen, Wolfgang G Pfeifer, Yan Yi Chen, Franziska Blaeschke, Eric Shifrut, Shane Vedova, Murad R Mamedov, Jing-Yi Jing Chung, Hong Li, Ruby Yu, David Wu, Jeffrey Wolf, Thomas G Martin, Carlos E Castro, Lumeng Ye,

Molecular basis for potent B cell responses to antigen displayed on particles of viral size

细胞对病毒大小颗粒上抗原产生强烈反应的分子基础

Jeremy F Brooks #, Julianne Riggs #, James L Mueller, Raisa Mathenge, Wei-Yun Wholey, Alexander R Meyer, Sekou-Tidiane Yoda, Vivasvan S Vykunta, Hailyn V Nielsen, Wei Cheng, Julie Zikherman

Peptide-mediated delivery of CRISPR enzymes for the efficient editing of primary human lymphocytes

肽介导的 CRISPR 酶递送可有效编辑原代人类淋巴细胞

Dana V Foss #, Joseph J Muldoon #, David N Nguyen #, Daniel Carr, Srishti U Sahu, John M Hunsinger, Stacia K Wyman, Netravathi Krishnappa, Rima Mendonsa, Elaine V Schanzer, Brian R Shy, Vivasvan S Vykunta, Vincent Allain, Zhongmei Li, Alexander Marson, Justin Eyquem, Ross C Wilson

Hedgehog target genes regulate lipid metabolism to drive basal cell carcinoma and medulloblastoma

Hedgehog 靶基因调节脂质代谢以驱动基底细胞癌和髓母细胞瘤

Vikas Daggubati, Akshara Vykunta, Abrar Choudhury, Zulekha Qadeer, Kanish Mirchia, Olivier Saulnier, Naomi Zakimi, Kelly Hines, Michael Paul, Linyu Wang, Natalia Jura, Libin Xu, Jeremy Reiter, Michael Taylor, William Weiss, David Raleigh

CRISPR-Cas9-mediated nuclear transport and genomic integration of nanostructured genes in human primary cells

利用 CRISPR-Cas9 介导的纳米结构基因在人类原代细胞中的核转运和基因组整合

Enrique Lin-Shiao ,Wolfgang G Pfeifer ,Brian R Shy ,Mohammad Saffari Doost ,Evelyn Chen ,Vivasvan S Vykunta ,Jennifer R Hamilton ,Elizabeth C Stahl ,Diana M Lopez ,Cindy R Sandoval Espinoza ,Alexander E Deyanov ,Rachel J Lew ,Michael G Poirer ,Alexander Marson ,Carlos E Castro ,Jennifer A Doudna