日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Author Correction: Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

作者更正:鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

One-Dimensional Polycyclic Aromatic Hydrocarbons Incorporating Multiple Dithiafulvene Units-Novel Multi-Redox and Electrochromic Systems

含有多个二硫代富烯单元的一维多环芳烃——新型多重氧化还原和电致变色体系

Rindom, Cecilie; Seljmani, Florim; Woodcock, Lukas Bradley; Nielsen, Mogens Brøndsted

Deficiency of Smooth Muscle Adar1 Exacerbates Vascular Remodeling and Pulmonary Hypertension

平滑肌Adar1缺乏会加剧血管重塑和肺动脉高压

Kim, Yunhye; Maroli, Giovanni; Woodcock, Chen-Shan Chen; Kim, Hyunbum; Liu, Yu; Klouda, Tim; Li, Yan; Li, Qin; Hao, Yuan; Schumacher, Valerie; Turton, Helena A; Thompson, A A Roger; Looso, Mario; Kuenne, Carsten; Valasarajan, Chanil; Ruppert, Clemens; Avolio, Theodore; Tang, Ying; Tai, Yi-Yin; Kudryashova, Tatiana V; Goncharova, Elena A; Wu, Joseph C; Li, Jin Billy; Bertero, Thomas; Savai, Rajkumar; Raby, Benjamin A; Chan, Stephen Y; Pullamsetti, Soni S; Yuan, Ke

Endothelial ADAR1 Deficit Induces the NOCT-IRF7 Axis in Pulmonary Hypertension

内皮细胞ADAR1缺陷诱导肺动脉高压中的NOCT-IRF7轴激活

Woodcock, Chen-Shan Chen; Maroli, Giovanni; Kim, Hyunbum; Tai, Yi Yin; Tang, Ying; Okawa, Satoshi; Homsi, Rami; Kim, Yunhye; Cho, Shu-Ting; Jiang, Siyi; Chauvet, Caroline; Wang, Bing; Al Aaraj, Yassmin; Lafyatis, Robert; Saggar, Rajan; Sembrat, John; Wang, Qingde; Li, Qin; Frump, Andrea L; Lahm, Tim; McCubbrey, Alexandra L; Kudryashova, Tatiana V; Goncharova, Elena A; Nouraie, Seyed Mehdi; Bertero, Thomas; Yuan, Ke; Pullamsetti, Soni S; Chan, Stephen Y

PET/CT imaging of tuberculosis lung lesions in marmosets treated with different drug regimens aligns with human clinical outcomes

对接受不同药物治疗方案的狨猴进行结核性肺部病变的PET/CT成像,结果与人类临床疗效相符。

Greenstein, Talia; Via, Laura E; Moraes, Mariana Pereira; Weiner, Danielle M; Dayao, Emmanuel K; Walker, April M; Abdi, Ayan; Fleegle, Joel D; Gomez, Felipe; Repoli, Katelyn M; Woodcock, Michael J; Boshoff, Helena I M; Egbelowo, Oluwaseun; Gausi, Kamunkhwala; Denti, Paolo; Kaya, Firat; Zimmerman, Matthew; Miller, Eric L; Dartois, Véronique A; Barry, Clifton E 3rd; Aldridge, Bree B

Response to the FDA's proposed pathway for individualized genetic therapies

对FDA提出的个体化基因治疗途径的回应

Yu, Timothy W; Vitarello, Julia; Musunuru, Kiran; Ahrens-Nicklas, Rebecca C; Liu, David R; Mellion, Michelle L; Urnov, Fyodor; Yan, Winston; Chunduru, Srinivas; Barrett, David; Flotte, Terence R; Woodcock, Janet

Reconciling links between diversity and population stability across global plant communities

协调全球植物群落多样性与种群稳定性之间的联系

Pan, Xiaobin; Hautier, Yann; Lepš, Jan; Wang, Shaopeng; Barry, Kathryn E; Bazzichetto, Manuele; Chelli, Stefano; Doležal, Jiří; Eisenhauer, Nico; Essl, Franz; Fischer, Felícia M; Godoy, Oscar; Gómez-García, Daniel; Götzenberger, Lars; Gracia, Clara; Guido, Anaclara; Hallett, Lauren M; Harrison, Susan; He, Miao; Hector, Andrew; Hong, Pubin; Isbell, Forest; Kowalchuk, George A; Lecegui, Victor; Li, Xiaofei; Liang, Maowei; Louault, Frédérique; Májeková, Maria; Marrs, Rob; Mohanbabu, Neha; Mori, Akira S; Pakeman, Robin J; Paquette, Alain; Peco, Begoña; Peñuelas, Josep; Pillar, Valério D; Rueda, Marta; Schmidt, Wolfgang; Segrestin, Jules; Sperandii, Marta Gaia; Valencia, Enrique; Vandvik, Vigdis; Wang, Shengnan; Ward, David; Wiser, Susan; Woodcock, Ben A; Xu, Chong; Young, Truman; Yu, Fei-Hai; Zheng, Liting; Zhong, Zhiwei; de Bello, Francesco

Expert perspectives on exposure-response functions for urban health policy: Lessons from a UBDPolicy workshop

专家对城市健康政策暴露-反应函数的看法:来自UBDPolicy研讨会的经验教训

Williams, Harry; Andersen, Zorana Jovanovic; Boogaard, Hanna; Brage, Søren; Browning, Matthew H E M; Cai, Samuel; Chen, Xuan; deSouza, Priyanka; Dzhambov, Angel M; Fenech, Benjamin; Flower, Gillian; Forastiere, Francesco; Garcia, Leandro; Gasparrini, Antonio; Gehring, Ulrike; Gowers, Alison M; Hoek, Gerard; Khomenko, Sasha; Lim, Chris C; Lu, Chenxi; Mitsakou, Christina; Pozzer, Andrea; Ramani, Tara; Roscoe, Charlotte; Spadaro, Joseph V; Tatah, Lambed; Vienneau, Danielle; Woodcock, James; Yeager, Ray; Zapata-Diomedi, Belen; Nieuwenhuijsen, Mark; Khreis, Haneen

Jasmonate signaling and prey nutrient availability trigger distinct biochemical responses in the Drosera capensis feeding cycle

茉莉酸信号和猎物营养物质的可用性会引发茅膏菜(Drosera capensis)摄食周期中不同的生化反应。

Long, Zane G; Takahashi, Gemma R; Cumpio, Franchesca M; Akbari, Omar J; Castelan, Ulysses; Hadadian, Mark; Le, Jonathan V; Alemayhu, Aden M; Einstein, David E; Einstein, Elliot E; Kelz, Jessica I; Kwok, Ashley O; Pineda, Allison; Shabakesaz, Pauniz; Unhelkar, Megha H; Woodcock, Sofiya M; Butts, Carter T; Martin, Rachel W