Quantifying and mitigating motor phenotypes induced by antisense oligonucleotides in the central nervous system
量化和减轻中枢神经系统中反义寡核苷酸诱导的运动表型
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.10.024
Moazami, Michael P; Rembetsy-Brown, Julia M; Sarli, Samantha L; McEachern, Holly R; Wang, Feng; Ohara, Masahiro; Wagh, Atish; Kelly, Karen; Krishnamurthy, Pranathi Meda; Weiss, Alexandra; Marosfoi, Miklos; King, Robert M; Motwani, Mona; Gray-Edwards, Heather; Fitzgerald, Katherine A; Brown, Robert H; Watts, Jonathan K