Benefit of burosumab in adults with X-linked hypophosphataemia (XLH) is maintained with long-term treatment
长期治疗可维持布罗索单抗对患有X连锁低磷血症(XLH)成人患者的疗效。
期刊:RMD Open
影响因子:4.7
doi:10.1136/rmdopen-2022-002676
Kamenicky, Peter; Briot, Karine; Brandi, Maria Luisa; Cohen-Solal, Martine; Crowley, Rachel K; Keen, Richard; Kolta, Sami; Lachmann, Robin H; Lecoq, Anne-Lise; Ralston, Stuart H; Walsh, Jennifer S; Rylands, Angela J; Williams, Angela; Sun, Wei; Nixon, Annabel; Nixon, Mark; Javaid, Muhammad K