AAV-mediated rescue of Eps8 expression in vivo restores hair-cell function in a mouse model of recessive deafness
AAV 介导的 Eps8 表达体内挽救可恢复隐性耳聋小鼠模型中的毛细胞功能
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2022.07.012
Jing-Yi Jeng, Adam J Carlton, Richard J Goodyear, Colbie Chinowsky, Federico Ceriani, Stuart L Johnson, Tsung-Chang Sung, Yelena Dayn, Guy P Richardson, Michael R Bowl, Steve D M Brown, Uri Manor, Walter Marcotti